Search Results - "Burnight ER"

Production of clinical grade patient iPSC-derived 3D retinal organoids containing transplantable photoreceptor cells.

Authors: Bohrer, Laura R. Wiley, Luke A. Wright, Allison T. et al.

Source: Stem Cell Research & Therapy. 11/17/2025, Vol. 16 Issue 1, p1-16. 16p.

Inherited retinal degeneration in Malay and Indian populations of Singapore and Malaysia: a prospective multicentre study.

Authors: Sao Su, Sandy Chan, Choi Mun Bylstra, Yasmin et al.

Source: Ophthalmic Genetics. Jun2025, Vol. 46 Issue 3, p225-236. 12p.

Characterization of large transgene integrations in Chinese hamster ovary cells using a bioengineered mammalian transposase.

Authors: Marx, Nicolas Otte, Anna‐Maria Leitner, Klaus et al.

Source: Biotechnology Progress. May/Jun2025, Vol. 41 Issue 3, p1-13. 13p.

AAV-based gene therapies for neovascular AMD.

Authors: Kim TH Kwon CY Song JY et al.

Source: Gene therapy [Gene Ther] 2026 Feb 13. Date of Electronic Publication: 2026 Feb 13.

Publication Type: Journal Article; Review

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE

Comprehensive multiomics analyses identify guanylate cyclase activator 1A as a photoreceptor-specific target in a murine model of oxygen-induced retinopathy.

Authors: Yang Q Wang J Wu T et al.

Source: Journal of translational medicine [J Transl Med] 2026 Apr 29; Vol. 24 (1). Date of Electronic Publication: 2026 Apr 29.

Publication Type: Journal Article

Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 101190741 Publication Model: Electronic Cited Medium: Internet ISSN: 1479-5876 (Electronic) Linking ISSN: 14795876 NLM ISO Abbreviation: J Transl Med Subsets: MEDLINE

AAV Capsid Modification and Its Influence on Viral Protein Stoichiometry and Packaging Fitness: Current Understandings and Future Direction.

Authors: Dogbey, Dennis Makafui Barth, Stefan

Source: Molecular Biotechnology. Jan2026, Vol. 68 Issue 1, p62-70. 9p.

Generation of transgenic pigs with targeted insertion of a wildtype copy of human PKD2 gene.

Authors: Zhang XL Luo JN Cao Y et al.

Source: Molecular biology reports [Mol Biol Rep] 2026 Jun 23; Vol. 53 (1). Date of Electronic Publication: 2026 Jun 23.

Publication Type: Journal Article

Journal Info: Publisher: Reidel Country of Publication: Netherlands NLM ID: 0403234 Publication Model: Electronic Cited Medium: Internet ISSN: 1573-4978 (Electronic) Linking ISSN: 03014851 NLM ISO Abbreviation: Mol Biol Rep Subsets: MEDLINE

Assessment of F/HN-pseudotyped lentiviral vector following intravenous delivery to mice.

Authors: Bell RV Faulkner NB Sinadinos A et al.

Source: Gene therapy [Gene Ther] 2026 Jun 18. Date of Electronic Publication: 2026 Jun 18.

Publication Type: Journal Article

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE

Engineered APP C-terminus Alters Its Native Transcript Dynamics in Differentiated SH-SY5Y-Derived Neurons.

Authors: Kulatunga DCM Ranaraja U Kim EY et al.

Source: Molecular neurobiology [Mol Neurobiol] 2026 May 19; Vol. 63 (1). Date of Electronic Publication: 2026 May 19.

Publication Type: Journal Article

Journal Info: Publisher: Humana Press Country of Publication: United States NLM ID: 8900963 Publication Model: Electronic Cited Medium: Internet ISSN: 1559-1182 (Electronic) Linking ISSN: 08937648 NLM ISO Abbreviation: Mol Neurobiol Subsets: MEDLINE

Direct reprogramming of Müller glia into photoreceptors via multiple transcription factors and small molecules: molecular mechanisms and transcriptomic analysis.

Authors: Endo Y Sugano E Seko Y et al.

Source: In vitro cellular & developmental biology. Animal [In Vitro Cell Dev Biol Anim] 2026 May; Vol. 62 (5), pp. 685-703. Date of Electronic Publication: 2026 Feb 25.

Publication Type: Journal Article

Journal Info: Publisher: Springer Country of Publication: Germany NLM ID: 9418515 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1543-706X (Electronic) Linking ISSN: 10712690 NLM ISO Abbreviation: In Vitro Cell Dev Biol Anim Subsets: MEDLINE

Repurposing of the enhancer-promoter communication underlies the compensation of Mesp2 by Mesp1.

Authors: Okada, Hajime Saga, Yumiko

Source: PLoS Genetics. 1/13/2022, Vol. 18 Issue 1, p1-24. 24p.

Gene therapy shines light on congenital stationary night blindness for future cures.

Authors: Zhang, Yi Lin, Siqi Yu, Lingqi et al.

Source: Journal of Translational Medicine. 4/3/2025, Vol. 23, p1-26. 26p.

Endoplasmic reticulum stress and rhodopsin accumulation in an organoid model of Retinitis Pigmentosa carrying a RHO pathogenic variant.

Authors: Navinés-Ferrer, Arnau Pomares, Esther

Source: Stem Cell Research & Therapy. 2/14/2025, Vol. 16 Issue 1, p1-15. 15p.

A mammalian genomic signature shaped by single nucleotide variants regulates transcriptome integrity and diversity.

Authors: Yang J Ogunsola S Wong J et al.

Source: Genome biology [Genome Biol] 2026 Apr 29; Vol. 27 (1). Date of Electronic Publication: 2026 Apr 29.

Publication Type: Journal Article

Journal Info: Publisher: BioMed Central Ltd Country of Publication: England NLM ID: 100960660 Publication Model: Electronic Cited Medium: Internet ISSN: 1474-760X (Electronic) Linking ISSN: 14747596 NLM ISO Abbreviation: Genome Biol Subsets: MEDLINE

AAV-mediated gene replacement therapy for LRAT-associated retinitis pigmentosa: a proof-of-concept study in a patient-based rat model.

Authors: El-Kalaani AM Ten Brink JB Boon CJF et al.

Source: Gene therapy [Gene Ther] 2026 Mar 10. Date of Electronic Publication: 2026 Mar 10.

Publication Type: Journal Article

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE

Stem cell sources and characterization in the development of cell-based products for treating retinal disease: An NEI Town Hall report.

Authors: Fortress, Ashley M. Miyagishima, Kiyoharu J. Reed, Amberlynn A. et al.

Source: Stem Cell Research & Therapy. 3/29/2023, Vol. 14 Issue 1, p1-13. 13p.

Automating iPSC generation to enable autologous photoreceptor cell replacement therapy.

Authors: Bohrer, Laura R. Stone, Nicholas E. Mullin, Nathaniel K. et al.

Source: Journal of Translational Medicine. 2/28/2023, Vol. 21 Issue 1, p1-14. 14p.

Gellan gum as a promising transplantation carrier for differentiated progenitor cells in ophthalmic therapies.

Authors: Moyo, Mthabisi Talent George Adali, Terin

Source: Journal of Bioactive & Compatible Polymers. Jan2025, Vol. 40 Issue 1, p136-157. 22p.

biGMamAct: efficient CRISPR/Cas9-mediated docking of large functional DNA cargoes at the ACTB locus.

Authors: Pelosse, Martin Marcia, Marco

Source: Synthetic Biology (23977000). 2025, Vol. 10 Issue 1, p1-12. 12p.

AAV2/4-RS1 gene therapy in the retinoschisin knockout mouse model of X-linked retinoschisis.

Authors: Scruggs, Brittni A. Bhattarai, Sajag Helms, Megan et al.

Source: PLoS ONE. 12/7/2022, Vol. 17 Issue 12, p1-18. 18p.