Search Results - "Chamberlain JS"

Clinical implications of basic research. Cachexia in cancer -- zeroing in on myosin.

Authors: Chamberlain JS (AUTHOR)

Source: New England Journal of Medicine. 11/11/2004, Vol. 351 Issue 20, p2124-2125. 2p.

Sequencing protocols to genotype mdx, mdx(4cv), and mdx(5cv) mice.

Authors: Banks GB Combs AC Chamberlain JS et al.

Source: Muscle & Nerve. Aug2010, Vol. 42 Issue 2, p268-270. 3p.

On fixing broken muscle...fall seven times, stand up eight--Japanese proverb.

Authors: Carter GT Han JJ Chamberlain JR et al.

Source: Muscle & Nerve. Jun2010, Vol. 41 Issue 6, p737-739. 3p.

Dystrophins DP71 and DP427 determine cell viability during proliferation and myofibre differentiation.

Authors: Szwec S Durska A Kościelniak-Wawro P et al.

Source: Cell death & disease [Cell Death Dis] 2026 Apr 11; Vol. 17 (1). Date of Electronic Publication: 2026 Apr 11.

Publication Type: Journal Article

Journal Info: Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101524092 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-4889 (Electronic) NLM ISO Abbreviation: Cell Death Dis Subsets: MEDLINE

Quantitative MRI Assessment of Myotoxin-Induced Skeletal Muscle Damage of mdx Mice.

Authors: Vohra R Park J Zhang F et al.

Source: Muscle & nerve [Muscle Nerve] 2026 Aug; Vol. 74 (2), pp. 485-491. Date of Electronic Publication: 2026 Jun 06.

Publication Type: Journal Article

Journal Info: Publisher: John Wiley & Sons Country of Publication: United States NLM ID: 7803146 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1097-4598 (Electronic) Linking ISSN: 0148639X NLM ISO Abbreviation: Muscle Nerve Subsets: MEDLINE

Proteomics-based evaluation of AAV dystrophin gene therapy outcomes in mdx skeletal muscle.

Authors: Johnson EE Reyes TR Chamberlain JS et al.

Source: JCI insight [JCI Insight] 2025 Nov 27; Vol. 11 (2). Date of Electronic Publication: 2025 Nov 27 (Print Publication: 2026).

Publication Type: Journal Article

Journal Info: Publisher: American Society for Clinical Investigation Country of Publication: United States NLM ID: 101676073 Publication Model: eCollection Cited Medium: Internet ISSN: 2379-3708 (Electronic) Linking ISSN: 23793708 NLM ISO Abbreviation: JCI Insight Subsets: MEDLINE

Genetic strategies for therapy of Duchenne muscular dystrophy.

Authors: Łoboda A Chamberlain JS Dulak J

Source: Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2025 Oct 31; Vol. 36 (4), pp. 102759. Date of Electronic Publication: 2025 Oct 31 (Print Publication: 2025).

Publication Type: Journal Article; Review

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101581621 Publication Model: eCollection Cited Medium: Print ISSN: 2162-2531 (Print) Linking ISSN: 21622531 NLM ISO Abbreviation: Mol Ther Nucleic Acids Subsets: PubMed not MEDLINE

Bidirectional role of Costameres in the pathophysiology of mdx skeletal muscles.

Authors: Banks GB Bisset DR Chamberlain JS

Source: Human molecular genetics [Hum Mol Genet] 2025 Oct 05; Vol. 34 (20), pp. 1681-1692.

Publication Type: Journal Article

Journal Info: Publisher: IRL Press at Oxford University Press Country of Publication: England NLM ID: 9208958 Publication Model: Print Cited Medium: Internet ISSN: 1460-2083 (Electronic) Linking ISSN: 09646906 NLM ISO Abbreviation: Hum Mol Genet Subsets: MEDLINE

The future of gene therapy: Safer vectors, sharper focus: High-profile failures demand deep root cause analysis - but the transformative potential of AAV remains within reach if the field is willing to learn and evolve.

Authors: Chamberlain JS Davidson BL George LA et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2025 Oct 01; Vol. 33 (10), pp. 4694-4695. Date of Electronic Publication: 2025 Sep 12.

Publication Type: Journal Article

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE; In Process

Expression of full-length dystrophin reverses muscular dystrophy defects in young and old mdx4cv mice.

Authors: Tasfaout H McMillen TS Reyes TR et al.

Source: The Journal of clinical investigation [J Clin Invest] 2025 Jun 10; Vol. 135 (15). Date of Electronic Publication: 2025 Jun 10 (Print Publication: 2025).

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: American Society for Clinical Investigation Country of Publication: United States NLM ID: 7802877 Publication Model: eCollection Cited Medium: Internet ISSN: 1558-8238 (Electronic) Linking ISSN: 00219738 NLM ISO Abbreviation: J Clin Invest Subsets: MEDLINE

The road toward AAV-mediated gene therapy of Duchenne muscular dystrophy.

Authors: Bengtsson NE Tasfaout H Chamberlain JS

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2025 May 07; Vol. 33 (5), pp. 2035-2051. Date of Electronic Publication: 2025 Apr 02.

Publication Type: Journal Article; Review

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy.

Authors: Birch SM Lawlor MW Conlon TJ et al.

Source: Science translational medicine [Sci Transl Med] 2023 Jan 04; Vol. 15 (677), pp. eabo1815. Date of Electronic Publication: 2023 Jan 04.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

Journal Info: Publisher: American Association for the Advancement of Science Country of Publication: United States NLM ID: 101505086 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1946-6242 (Electronic) Linking ISSN: 19466234 NLM ISO Abbreviation: Sci Transl Med Subsets: MEDLINE

Correction: Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review.

Authors: Szwec S Kapłucha Z Chamberlain JS et al.

Source: BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy [BioDrugs] 2025 Jan; Vol. 39 (1), pp. 167.

Publication Type: Published Erratum

Journal Info: Publisher: Adis, Springer International Country of Publication: New Zealand NLM ID: 9705305 Publication Model: Print Cited Medium: Internet ISSN: 1179-190X (Electronic) Linking ISSN: 11738804 NLM ISO Abbreviation: BioDrugs Subsets: MEDLINE; PubMed not MEDLINE

Split intein-mediated protein trans-splicing to express large dystrophins.

Authors: Tasfaout H Halbert CL McMillen TS et al.

Source: Nature [Nature] 2024 Aug; Vol. 632 (8023), pp. 192-200. Date of Electronic Publication: 2024 Jul 17.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 0410462 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-4687 (Electronic) Linking ISSN: 00280836 NLM ISO Abbreviation: Nature Subsets: MEDLINE

Gene therapy delivered micro-dystrophins co-localize with transgenic utrophin in dystrophic skeletal muscle fibers.

Authors: Krishna S Piepho AB Lake DM et al.

Source: Neuromuscular disorders : NMD [Neuromuscul Disord] 2024 Mar; Vol. 36, pp. 1-5. Date of Electronic Publication: 2024 Jan 12.

Publication Type: Journal Article

Journal Info: Publisher: Pergamon Press Country of Publication: England NLM ID: 9111470 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1873-2364 (Electronic) Linking ISSN: 09608966 NLM ISO Abbreviation: Neuromuscul Disord Subsets: MEDLINE

Microutrophin expression in dystrophic mice displays myofiber type differences in therapeutic effects.

Authors: Banks GB Chamberlain JS Odom GL

Source: PLoS genetics [PLoS Genet] 2020 Nov 11; Vol. 16 (11), pp. e1009179. Date of Electronic Publication: 2020 Nov 11 (Print Publication: 2020).

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: Public Library of Science Country of Publication: United States NLM ID: 101239074 Publication Model: eCollection Cited Medium: Internet ISSN: 1553-7404 (Electronic) Linking ISSN: 15537390 NLM ISO Abbreviation: PLoS Genet Subsets: MEDLINE

Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review.

Authors: Szwec S Kapłucha Z Chamberlain JS et al.

Source: BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy [BioDrugs] 2024 Jan; Vol. 38 (1), pp. 95-119. Date of Electronic Publication: 2023 Nov 02.

Publication Type: Comparative Study; Journal Article; Review

Journal Info: Publisher: Adis, Springer International Country of Publication: New Zealand NLM ID: 9705305 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-190X (Electronic) Linking ISSN: 11738804 NLM ISO Abbreviation: BioDrugs Subsets: MEDLINE

In vivo selection of synthetic nucleocapsids for tissue targeting.

Authors: Olshefsky A Benasutti H Sylvestre M et al.

Source: Proceedings of the National Academy of Sciences of the United States of America [Proc Natl Acad Sci U S A] 2023 Nov 14; Vol. 120 (46), pp. e2306129120. Date of Electronic Publication: 2023 Nov 08.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: National Academy of Sciences Country of Publication: United States NLM ID: 7505876 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1091-6490 (Electronic) Linking ISSN: 00278424 NLM ISO Abbreviation: Proc Natl Acad Sci U S A Subsets: MEDLINE

Biomarkers for Duchenne muscular dystrophy progression: impact of age in the mdx tongue spared muscle.

Authors: Lorena MDSV Santos EKD Ferretti R et al.

Source: Skeletal muscle [Skelet Muscle] 2023 Sep 13; Vol. 13 (1), pp. 16. Date of Electronic Publication: 2023 Sep 13.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.; Research Support, N.I.H., Extramural

Journal Info: Publisher: BioMed Central Ltd Country of Publication: England NLM ID: 101561193 Publication Model: Electronic Cited Medium: Internet ISSN: 2044-5040 (Electronic) Linking ISSN: 20445040 NLM ISO Abbreviation: Skelet Muscle Subsets: MEDLINE

AAV-based gene therapies for the muscular dystrophies.

Authors: Crudele JM Chamberlain JS

Source: Human molecular genetics [Hum Mol Genet] 2019 Oct 01; Vol. 28 (R1), pp. R102-R107.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Review

Journal Info: Publisher: IRL Press at Oxford University Press Country of Publication: England NLM ID: 9208958 Publication Model: Print Cited Medium: Internet ISSN: 1460-2083 (Electronic) Linking ISSN: 09646906 NLM ISO Abbreviation: Hum Mol Genet Subsets: MEDLINE