Search Results - "Epstein, Benjamin E."

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  1. 1

    Comparison of neonatal systemic and intracerebroventricular AAV9 gene therapy delivery demonstrating improved behavioral and phenotypic outcomes in a mouse model of Niemann-Pick disease, type C1.

    Authors: Epstein, Benjamin E. Soden, Gabrielle M. Incao, Arturo A. et al.

    Source: PLoS ONE. 3/11/2026, Vol. 21 Issue 3, p1-20. 20p.

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  2. 2

    Combining Engineered Nucleases with Adeno-associated Viral Vectors for Therapeutic Gene Editing.

    Authors: Epstein BE Schaffer DV

    Source: Advances in experimental medicine and biology [Adv Exp Med Biol] 2017; Vol. 1016, pp. 29-42.

    Publication Type: Journal Article; Review

    Journal Info: Publisher: Kluwer Academic/Plenum Publishers Country of Publication: United States NLM ID: 0121103 Publication Model: Print Cited Medium: Print ISSN: 0065-2598 (Print) Linking ISSN: 00652598 NLM ISO Abbreviation: Adv Exp Med Biol Subsets: MEDLINE

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  3. 3

    Genome Engineering Using Adeno-associated Virus: Basic and Clinical Research Applications.

    Authors: Gaj T Epstein BE Schaffer DV

    Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2016 Mar; Vol. 24 (3), pp. 458-64. Date of Electronic Publication: 2015 Sep 16.

    Publication Type: Journal Article; Research Support, N.I.H., Extramural; Review

    Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

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