Search Results - "Halbert CL"

Expression of full-length dystrophin reverses muscular dystrophy defects in young and old mdx4cv mice.

Authors: Tasfaout H McMillen TS Reyes TR et al.

Source: The Journal of clinical investigation [J Clin Invest] 2025 Jun 10; Vol. 135 (15). Date of Electronic Publication: 2025 Jun 10 (Print Publication: 2025).

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: American Society for Clinical Investigation Country of Publication: United States NLM ID: 7802877 Publication Model: eCollection Cited Medium: Internet ISSN: 1558-8238 (Electronic) Linking ISSN: 00219738 NLM ISO Abbreviation: J Clin Invest Subsets: MEDLINE

Split intein-mediated protein trans-splicing to express large dystrophins.

Authors: Tasfaout H Halbert CL McMillen TS et al.

Source: Nature [Nature] 2024 Aug; Vol. 632 (8023), pp. 192-200. Date of Electronic Publication: 2024 Jul 17.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 0410462 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-4687 (Electronic) Linking ISSN: 00280836 NLM ISO Abbreviation: Nature Subsets: MEDLINE

Comparison of dystrophin expression following gene editing and gene replacement in an aged preclinical DMD animal model.

Authors: Bengtsson NE Crudele JM Klaiman JM et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2022 Jun 01; Vol. 30 (6), pp. 2176-2185. Date of Electronic Publication: 2022 Feb 08.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

Elimination of contaminating cap genes in AAV vector virions reduces immune responses and improves transgene expression in a canine gene therapy model.

Authors: Wang Z Halbert CL Lee D et al.

Source: Gene therapy [Gene Ther] 2014 Apr; Vol. 21 (4), pp. 363-70. Date of Electronic Publication: 2014 Feb 06.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE

Successful regional delivery and long-term expression of a dystrophin gene in canine muscular dystrophy: a preclinical model for human therapies.

Authors: Wang Z Storb R Halbert CL et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2012 Aug; Vol. 20 (8), pp. 1501-7. Date of Electronic Publication: 2012 Jun 12.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

Capsid-expressing DNA in AAV vectors and its elimination by use of an oversize capsid gene for vector production.

Authors: Halbert CL Metzger MJ Lam SL et al.

Source: Gene therapy [Gene Ther] 2011 Apr; Vol. 18 (4), pp. 411-7. Date of Electronic Publication: 2010 Dec 16.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE

Expression of human alpha1-antitrypsin in mice and dogs following AAV6 vector-mediated gene transfer to the lungs.

Authors: Halbert CL Madtes DK Vaughan AE et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2010 Jun; Vol. 18 (6), pp. 1165-72. Date of Electronic Publication: 2010 Apr 06.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

Sheep retrovirus structural protein induces lung tumours.

Authors: Wootton SK Halbert CL Miller AD

Source: Nature [Nature] 2005 Apr 14; Vol. 434 (7035), pp. 904-7.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 0410462 Publication Model: Print Cited Medium: Internet ISSN: 1476-4687 (Electronic) Linking ISSN: 00280836 NLM ISO Abbreviation: Nature Subsets: MEDLINE

Efficient mouse airway transduction following recombination between AAV vectors carrying parts of a larger gene.

Authors: Halbert CL Allen JM Miller AD

Source: Nature biotechnology [Nat Biotechnol] 2002 Jul; Vol. 20 (7), pp. 697-701.

Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.

Journal Info: Publisher: Nature America Publishing Country of Publication: United States NLM ID: 9604648 Publication Model: Print Cited Medium: Print ISSN: 1087-0156 (Print) Linking ISSN: 10870156 NLM ISO Abbreviation: Nat Biotechnol Subsets: MEDLINE

Adeno-associated virus vector transduction of vascular smooth muscle cells in vivo.

Authors: Richter M Iwata A Nyhuis J et al.

Source: Physiological genomics [Physiol Genomics] 2000 Apr 27; Vol. 2 (3), pp. 117-27. Date of Electronic Publication: 2000 Apr 27.

Publication Type: Journal Article

Journal Info: Publisher: American Physiological Society Country of Publication: United States NLM ID: 9815683 Publication Model: Electronic Cited Medium: Internet ISSN: 1531-2267 (Electronic) Linking ISSN: 10948341 NLM ISO Abbreviation: Physiol Genomics Subsets: MEDLINE

AAV6 Vector Production and Purification for Muscle Gene Therapy.

Authors: Halbert CL Allen JM Chamberlain JS

Source: Methods in molecular biology (Clifton, N.J.) [Methods Mol Biol] 2018; Vol. 1687, pp. 257-266.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural

Journal Info: Publisher: Humana Press Country of Publication: United States NLM ID: 9214969 Publication Model: Print Cited Medium: Internet ISSN: 1940-6029 (Electronic) Linking ISSN: 10643745 NLM ISO Abbreviation: Methods Mol Biol Subsets: MEDLINE

Lung cancer in mice induced by the jaagsiekte sheep retrovirus envelope protein is not maintained by rare cancer stem cells, but tumorigenicity does correlate with Wnt pathway activation.

Authors: Vaughan AE Halbert CL Wootton SK et al.

Source: Molecular cancer research : MCR [Mol Cancer Res] 2012 Jan; Vol. 10 (1), pp. 86-95. Date of Electronic Publication: 2011 Nov 07.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

Journal Info: Publisher: American Association for Cancer Research Country of Publication: United States NLM ID: 101150042 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1557-3125 (Electronic) Linking ISSN: 15417786 NLM ISO Abbreviation: Mol Cancer Res Subsets: MEDLINE

Jaagsiekte sheep retrovirus and enzootic nasal tumor virus promoters drive gene expression in all airway epithelial cells of mice but only induce tumors in the alveolar region of the lungs.

Authors: Yu DL Linnerth-Petrik NM Halbert CL et al.

Source: Journal of virology [J Virol] 2011 Aug; Vol. 85 (15), pp. 7535-45. Date of Electronic Publication: 2011 May 18.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

Journal Info: Publisher: American Society For Microbiology Country of Publication: United States NLM ID: 0113724 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1098-5514 (Electronic) Linking ISSN: 0022538X NLM ISO Abbreviation: J Virol Subsets: MEDLINE

High-efficiency promoter-dependent transduction by adeno-associated virus type 6 vectors in mouse lung.

Authors: Halbert CL Lam SL Miller AD

Source: Human gene therapy [Hum Gene Ther] 2007 Apr; Vol. 18 (4), pp. 344-54.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: M.A. Liebert Country of Publication: United States NLM ID: 9008950 Publication Model: Print Cited Medium: Print ISSN: 1043-0342 (Print) Linking ISSN: 10430342 NLM ISO Abbreviation: Hum Gene Ther Subsets: MEDLINE

Envelope proteins of Jaagsiekte sheep retrovirus and enzootic nasal tumor virus induce similar bronchioalveolar tumors in lungs of mice.

Authors: Wootton SK Halbert CL Miller AD

Source: Journal of virology [J Virol] 2006 Sep; Vol. 80 (18), pp. 9322-5.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

Journal Info: Publisher: American Society For Microbiology Country of Publication: United States NLM ID: 0113724 Publication Model: Print Cited Medium: Print ISSN: 0022-538X (Print) Linking ISSN: 0022538X NLM ISO Abbreviation: J Virol Subsets: MEDLINE

Prevalence of neutralizing antibodies against adeno-associated virus (AAV) types 2, 5, and 6 in cystic fibrosis and normal populations: Implications for gene therapy using AAV vectors.

Authors: Halbert CL Miller AD McNamara S et al.

Source: Human gene therapy [Hum Gene Ther] 2006 Apr; Vol. 17 (4), pp. 440-7.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: M.A. Liebert Country of Publication: United States NLM ID: 9008950 Publication Model: Print Cited Medium: Print ISSN: 1043-0342 (Print) Linking ISSN: 10430342 NLM ISO Abbreviation: Hum Gene Ther Subsets: MEDLINE

Adeno-associated virus types 5 and 6 use distinct receptors for cell entry.

Authors: Seiler MP Miller AD Zabner J et al.

Source: Human gene therapy [Hum Gene Ther] 2006 Jan; Vol. 17 (1), pp. 10-9.

Publication Type: Comparative Study; Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: M.A. Liebert Country of Publication: United States NLM ID: 9008950 Publication Model: Print Cited Medium: Print ISSN: 1043-0342 (Print) Linking ISSN: 10430342 NLM ISO Abbreviation: Hum Gene Ther Subsets: MEDLINE

Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6.

Authors: Blankinship MJ Gregorevic P Allen JM et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2004 Oct; Vol. 10 (4), pp. 671-8.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print Cited Medium: Print ISSN: 1525-0016 (Print) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

Jaagsiekte sheep retrovirus envelope efficiently pseudotypes human immunodeficiency virus type 1-based lentiviral vectors.

Authors: Liu SL Halbert CL Miller AD

Source: Journal of virology [J Virol] 2004 Mar; Vol. 78 (5), pp. 2642-7.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

Journal Info: Publisher: American Society For Microbiology Country of Publication: United States NLM ID: 0113724 Publication Model: Print Cited Medium: Print ISSN: 0022-538X (Print) Linking ISSN: 0022538X NLM ISO Abbreviation: J Virol Subsets: MEDLINE

AAV-mediated gene transfer to mouse lungs.

Authors: Halbert CL Miller AD

Source: Methods in molecular biology (Clifton, N.J.) [Methods Mol Biol] 2004; Vol. 246, pp. 201-12.

Publication Type: Journal Article

Journal Info: Publisher: Humana Press Country of Publication: United States NLM ID: 9214969 Publication Model: Print Cited Medium: Print ISSN: 1064-3745 (Print) Linking ISSN: 10643745 NLM ISO Abbreviation: Methods Mol Biol Subsets: MEDLINE