Search Results - "Pipe SW"

Author Index.

Source: Haemophilia. Jun2020 Supplement S4, Vol. 26, p141-149. 9p.

A single amino acid variant in the variable region I of AAV capsid confers liver detargeting.

Authors: Xing, Ruxiao Xu, Mengyao Reil, Darcy et al.

Source: PLoS Pathogens. 9/17/2025, Vol. 21 Issue 9, p1-16. 16p.

Gene therapy for haemophilia A and B, from basic principles to clinical implementation: An illustrated review.

Authors: Ay, Cihan Frenzel, Laurent Pinachyan, Karen et al.

Source: Haemophilia. Jan2024, Vol. 30 Issue 1, p5-15. 11p.

A Phase 1/2, Open-Label, Single-Dose, Multicenter Study to Evaluate the Pharmacokinetics and Safety of Human Plasma-Derived Protein C Concentrate in Japanese Patients with Severe Congenital Protein C Deficiency (SCPCD).

Authors: Koh, Katsuyoshi Nogami, Keiji Kakuda, Harumi et al.

Source: Journal of Blood Medicine. Mar2026, p1-9. 9p.

Author Index.

Source: Haemophilia. Feb2021 Supplement S2, Vol. 27, p182-192. 11p.

A comprehensive care pathway of gene therapy for hemophilia based on current guideline documents and summary of product characteristics: communication from the ISTH SSC working group on gene therapy.

Authors: Mussert CMA Miesbach W Chowdary P et al.

Source: Journal of thrombosis and haemostasis : JTH [J Thromb Haemost] 2026 Feb; Vol. 24 (2), pp. 747-765. Date of Electronic Publication: 2025 Oct 27.

Publication Type: Journal Article; Review; Practice Guideline

Journal Info: Publisher: Elsevier Country of Publication: England NLM ID: 101170508 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1538-7836 (Electronic) Linking ISSN: 15387836 NLM ISO Abbreviation: J Thromb Haemost Subsets: MEDLINE

Genotype-directed Targeted Therapy for Pediatric Vascular Malformations: A Systematic Review.

Authors: Kumar, Bitesh Patil, Nidhi Goel, Prabudh et al.

Source: Journal of Indian Association of Pediatric Surgeons. Jul/Aug2026, Vol. 31 Issue 4, p513-524. 12p.

A retrospective study of rehabilitation for patients with hemophilia knee osteoarthritis after total knee arthroplasty: a 10 year cohort study.

Authors: Jin, Zhaokai Tang, Yi Yan, Kun et al.

Source: BMC Musculoskeletal Disorders. 11/13/2025, Vol. 26 Issue 1, p1-10. 10p.

Synovial Gene expression after Hemarthrosis differs between FVIII-deficient mice treated with recombinant FVIII or FVIII-Fc Fusion Protein.

Authors: Chumappumkal Joseph, Bilgimol Whisenant, Thomas C. Cooke, Esther J. et al.

Source: PLoS ONE. 5/19/2025, Vol. 20 Issue 5, p1-18. 18p.

WFH Guidelines for the Management of Hemophilia, 3rd edition.

Authors: Srivastava A Santagostino E Dougall A et al.

Corporate Authors: Srivastava A Santagostino E Dougall A et al.

Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2020 Aug; Vol. 26 Suppl 6, pp. 1-158. Date of Electronic Publication: 2020 Aug 03.

Publication Type: Journal Article; Practice Guideline

Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE

Content Validity of the Hemophilia Device Handling and Preference Assessment Questionnaire - A Cognitive Debrief Study in Patients with Hemophilia and Their Caregivers.

Authors: Rasmussen, Niklas Kahr Shah, Sanket Tsai, Jui-Hua et al.

Source: Patient Preference & Adherence. Sep2025, Vol. 19, p2807-2816. 10p.

Prevalence of COVID‐19 related hospitalizations and mortality in adults aged ≥40 years with haemophilia: A survey from Europe.

Authors: Hermans, Cedric Astermark, Jan Carvalho, Manuela et al.

Source: Haemophilia. May2023, Vol. 29 Issue 3, p913-916. 4p. 2 Charts.

Acute safety, cardiovascular, perceptual and neuromuscular responses to autoregulated and non-autoregulated blood flow restriction training during elbow rehabilitation in people with hemophilia.

Authors: Ogrezeanu, Daniel C. Tur-Boned, Andrea Rolnick, Nicholas et al.

Source: Frontiers in Sports & Active Living. 2025, p1-11.

Knowledge mapping and bibliometric insights into gene therapy for rare inherited hematologic pathologies: focus on sickle cell disease, hemophilia, and thalassemia.

Authors: Sweileh, Moutaz W.^1,2 (AUTHOR) moutazsweileh@najah.edu

Source: Orphanet Journal of Rare Diseases. 11/4/2025, Vol. 20 Issue 1, p1-16. 16p.

Evaluating the Cost-Effectiveness of Etranacogene Dezaparvovec Gene Therapy for Hemophilia B Treatment in the USA.

Authors: Sarker J Tice JA Rind DM et al.

Source: Applied health economics and health policy [Appl Health Econ Health Policy] 2025 May; Vol. 23 (3), pp. 467-478. Date of Electronic Publication: 2024 Dec 02.

Publication Type: Journal Article

Journal Info: Publisher: Open Mind Journals Ltd Country of Publication: New Zealand NLM ID: 101150314 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-1896 (Electronic) Linking ISSN: 11755652 NLM ISO Abbreviation: Appl Health Econ Health Policy Subsets: MEDLINE

Breaking barriers in haemophilia A care: One‐year real‐world experience with emicizumab prophylaxis at Civil Service Hospital, Kathmandu, Nepal.

Authors: Poudyal, Bishesh Sharma Bajracharya, Nikesh Paudel, Bishal et al.

Source: Haemophilia. Mar2025, Vol. 31 Issue 2, p328-330. 3p.

Bleed treatment with eptacog beta (rFVIIa) results in a low incidence of rebleeding in adult and adolescent patients with haemophilia A or B with inhibitors.

Authors: Dunn, Amy Dargaud, Yesim Abajas, Yasmina et al.

Source: Haemophilia. Jan2025, Vol. 31 Issue 1, p78-86. 9p.

Expert opinion paper on the treatment of hemophilia A with emicizumab.

Authors: López-Jaime, Francisco-José Benítez, Olga Díaz Jordán, Bolívar Luis et al.

Source: Hematology. Dec2023, Vol. 28 Issue 1, p1-7. 7p.

Accurate evaluation of factor VIII activity of efanesoctocog alfa in the presence of emicizumab.

Authors: Nougier C Pipe SW Pabinger I et al.

Source: Journal of thrombosis and haemostasis : JTH [J Thromb Haemost] 2025 May; Vol. 23 (5), pp. 1516-1521. Date of Electronic Publication: 2025 Jan 09.

Publication Type: Journal Article; Multicenter Study

Journal Info: Publisher: Elsevier Country of Publication: England NLM ID: 101170508 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1538-7836 (Electronic) Linking ISSN: 15387836 NLM ISO Abbreviation: J Thromb Haemost Subsets: MEDLINE

Neonatal Bleeding: A Single-center Egyptian NICU Cross-Sectional Study.

Authors: Abdelwahab, Magy Ezz eldin, Zahraa Mohamed Elansary, Mervat Mohamed et al.

Source: Iranian Journal of Neonatology. 2026, Vol. 17 Issue 3, p30-36. 7p.