Search Results - "Small JC"

Cardiotoxic Effects and Microdystrophin Expression after Gene Therapy for DMD.

Authors: Samelson-Jones BJ Martos-Rus C Yrigollen CM et al.

Source: The New England journal of medicine [N Engl J Med] 2026 Jul 22. Date of Electronic Publication: 2026 Jul 22.

Publication Type: Letter

Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE

Neuroepithelial Tumor with AAV Integration after Intracisternal Magna Vector Delivery.

Authors: Ahrens-Nicklas RC Kotch C Roche AM et al.

Source: The New England journal of medicine [N Engl J Med] 2026 Jun 04; Vol. 394 (21), pp. 2126-2133. Date of Electronic Publication: 2026 May 13.

Publication Type: Journal Article; Case Reports

Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE

Real-world outcomes of delandistrogene moxeparvovec gene therapy: Motor outcomes and emerging safety concerns.

Authors: Keselman DJ Small JC Seneviratne T et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2026 Jan 07; Vol. 34 (1), pp. 123-130. Date of Electronic Publication: 2025 Oct 04.

Publication Type: Journal Article

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

KD025 Is a Casein Kinase 2 Inhibitor That Protects Against Glucolipotoxicity in β-Cells.

Authors: Devkota R Small JC Carbone K et al.

Source: Diabetes [Diabetes] 2024 Apr 01; Vol. 73 (4), pp. 585-591.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: American Diabetes Association Country of Publication: United States NLM ID: 0372763 Publication Model: Print Cited Medium: Internet ISSN: 1939-327X (Electronic) Linking ISSN: 00121797 NLM ISO Abbreviation: Diabetes Subsets: MEDLINE

Use of CD19-targeted immune modulation to eradicate AAV-neutralizing antibodies.

Authors: Doshi BS Markmann CA Novak N et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2025 Jul 02; Vol. 33 (7), pp. 3073-3085. Date of Electronic Publication: 2025 Mar 08.

Publication Type: Journal Article

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease.

Authors: Musunuru K Grandinette SA Wang X et al.

Source: The New England journal of medicine [N Engl J Med] 2025 Jun 12; Vol. 392 (22), pp. 2235-2243. Date of Electronic Publication: 2025 May 15.

Publication Type: Journal Article; Case Reports

Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE

Roctavian gene therapy for hemophilia A.

Authors: Samelson-Jones BJ Small JC George LA

Source: Blood advances [Blood Adv] 2024 Oct 08; Vol. 8 (19), pp. 5179-5189.

Publication Type: Journal Article; Review

Journal Info: Publisher: American Society of Hematology Country of Publication: United States NLM ID: 101698425 Publication Model: Print Cited Medium: Internet ISSN: 2473-9537 (Electronic) Linking ISSN: 24739529 NLM ISO Abbreviation: Blood Adv Subsets: MEDLINE

Subtype-selective prenylated isoflavonoids disrupt regulatory drivers of MYCN-amplified cancers.

Authors: Stokes ME Vasciaveo A Small JC et al.

Source: Cell chemical biology [Cell Chem Biol] 2024 Apr 18; Vol. 31 (4), pp. 805-819.e9. Date of Electronic Publication: 2023 Dec 06.

Publication Type: Journal Article

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101676030 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2451-9448 (Electronic) Linking ISSN: 24519448 NLM ISO Abbreviation: Cell Chem Biol Subsets: MEDLINE

The complete mitochondrial genome of the brown pansy butterfly, Junonia stygia (Aurivillius, 1894), (Insecta: Lepidoptera: Nymphalidae).

Authors: Ajibola S Arya V Barker EN et al.

Corporate Authors: Ajibola S Arya V Barker EN et al.

Source: Mitochondrial DNA. Part B, Resources [Mitochondrial DNA B Resour] 2019 Dec 09; Vol. 5 (1), pp. 41-43. Date of Electronic Publication: 2019 Dec 09.

Publication Type: Journal Article

Journal Info: Publisher: Taylor & Francis Country of Publication: England NLM ID: 101676334 Publication Model: Electronic Cited Medium: Internet ISSN: 2380-2359 (Electronic) Linking ISSN: 23802359 NLM ISO Abbreviation: Mitochondrial DNA B Resour Subsets: PubMed not MEDLINE

Phenotypic Screening for Small Molecules that Protect β-Cells from Glucolipotoxicity.

Authors: Small JC Joblin-Mills A Carbone K et al.

Source: ACS chemical biology [ACS Chem Biol] 2022 May 20; Vol. 17 (5), pp. 1131-1142. Date of Electronic Publication: 2022 Apr 19.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: American Chemical Society Country of Publication: United States NLM ID: 101282906 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1554-8937 (Electronic) Linking ISSN: 15548929 NLM ISO Abbreviation: ACS Chem Biol Subsets: MEDLINE

Influenza virus specific CD8⁺ T cells exacerbate infection following high dose influenza challenge of aged mice.

Authors: Parzych EM DiMenna LJ Latimer BP et al.

Source: BioMed research international [Biomed Res Int] 2013; Vol. 2013, pp. 876314. Date of Electronic Publication: 2013 Sep 26.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: Wiley Country of Publication: United States NLM ID: 101600173 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2314-6141 (Electronic) NLM ISO Abbreviation: Biomed Res Int Subsets: MEDLINE

Vaccine-induced T cells provide partial protection against high-dose rectal SIVmac239 challenge of rhesus macaques.

Authors: Lasaro MO Haut LH Zhou X et al.

Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2011 Feb; Vol. 19 (2), pp. 417-26. Date of Electronic Publication: 2010 Nov 16.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

FVIII activity following FVIII protein infusion or FVIII gene transfer predicts the bleeding risk in hemophilia A rats.

Authors: Lövgren KM Larsen MS Zintner SM et al.

Source: Journal of thrombosis and haemostasis : JTH [J Thromb Haemost] 2020 Jul; Vol. 18 (7), pp. 1586-1597. Date of Electronic Publication: 2020 Apr 16.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: Elsevier Country of Publication: England NLM ID: 101170508 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1538-7836 (Electronic) Linking ISSN: 15387836 NLM ISO Abbreviation: J Thromb Haemost Subsets: MEDLINE

Mesenchymal subtype neuroblastomas are addicted to TGF-βR2/HMGCR-driven protein geranylgeranylation.

Authors: Stokes ME Small JC Vasciaveo A et al.

Source: Scientific reports [Sci Rep] 2020 Jul 01; Vol. 10 (1), pp. 10748. Date of Electronic Publication: 2020 Jul 01.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 101563288 Publication Model: Electronic Cited Medium: Internet ISSN: 2045-2322 (Electronic) Linking ISSN: 20452322 NLM ISO Abbreviation: Sci Rep Subsets: MEDLINE

The Development and Characterization of an scFv-Fc Fusion-Based Gene Therapy to Reduce the Psychostimulant Effects of Methamphetamine Abuse.

Authors: Hay CE Ewing LE Hambuchen MD et al.

Source: The Journal of pharmacology and experimental therapeutics [J Pharmacol Exp Ther] 2020 Jul; Vol. 374 (1), pp. 16-23. Date of Electronic Publication: 2020 Apr 03.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: Elsevier Country of Publication: Netherlands NLM ID: 0376362 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1521-0103 (Electronic) Linking ISSN: 00223565 NLM ISO Abbreviation: J Pharmacol Exp Ther Subsets: MEDLINE

Gene-based FVIIa prophylaxis modulates the spontaneous bleeding phenotype of hemophilia A rats.

Authors: Zintner SM Small JC Pavani G et al.

Source: Blood advances [Blood Adv] 2019 Feb 12; Vol. 3 (3), pp. 301-311.

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

Journal Info: Publisher: American Society of Hematology Country of Publication: United States NLM ID: 101698425 Publication Model: Print Cited Medium: Internet ISSN: 2473-9537 (Electronic) Linking ISSN: 24739529 NLM ISO Abbreviation: Blood Adv Subsets: MEDLINE

One amino acid in mouse activated factor VII defines its endothelial protein C receptor (EPCR) binding and modulates its EPCR-dependent hemostatic activity in vivo.

Authors: Pavani G Zintner SM Ivanciu L et al.

Source: Journal of thrombosis and haemostasis : JTH [J Thromb Haemost] 2017 Mar; Vol. 15 (3), pp. 507-512. Date of Electronic Publication: 2017 Feb 14.

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

Journal Info: Publisher: Elsevier Country of Publication: England NLM ID: 101170508 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1538-7836 (Electronic) Linking ISSN: 15387836 NLM ISO Abbreviation: J Thromb Haemost Subsets: MEDLINE

MTA Pulpotomies: A Long-Term Case Series Outcomes Assessment of Complicated Crown Fractures.

Authors: Witherspoon DE Regan JD Small JC

Source: Texas dental journal [Tex Dent J] 2017 Mar; Vol. 134 (3), pp. 166-175.

Publication Type: Journal Article

Journal Info: Publisher: Texas Dental Association Country of Publication: United States NLM ID: 2984821R Publication Model: Print Cited Medium: Print ISSN: 0040-4284 (Print) Linking ISSN: 00404284 NLM ISO Abbreviation: Tex Dent J

The effect of adenovirus-specific antibodies on adenoviral vector-induced, transgene product-specific T cell responses.

Authors: Small JC Haut LH Bian A et al.

Source: Journal of leukocyte biology [J Leukoc Biol] 2014 Nov; Vol. 96 (5), pp. 821-31. Date of Electronic Publication: 2014 Jul 31.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 8405628 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1938-3673 (Electronic) Linking ISSN: 07415400 NLM ISO Abbreviation: J Leukoc Biol Subsets: MEDLINE

Construction and characterization of E1- and E3-deleted adenovirus vectors expressing two antigens from two separate expression cassettes.

Authors: Small JC Kurupati RK Zhou X et al.

Source: Human gene therapy [Hum Gene Ther] 2014 Apr; Vol. 25 (4), pp. 328-38. Date of Electronic Publication: 2014 Mar 25.

Publication Type: Journal Article; Research Support, N.I.H., Extramural

Journal Info: Publisher: M.A. Liebert Country of Publication: United States NLM ID: 9008950 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1557-7422 (Electronic) Linking ISSN: 10430342 NLM ISO Abbreviation: Hum Gene Ther Subsets: MEDLINE