Safety of switching to Migalastat from enzyme replacement therapy in Fabry disease: Experience from the Phase 3 ATTRACT study.
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| Title: | Safety of switching to Migalastat from enzyme replacement therapy in Fabry disease: Experience from the Phase 3 ATTRACT study. |
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| Authors: | Hughes, Derralynn A.1, rmgvdah@ucl.ac.uk, Nicholls, Kathleen2, Sunder‐Plassmann, Gere3, Jovanovic, Ana4, Feldt‐Rasmussen, Ulla5, Schiffmann, Raphael6, Giugliani, Robert7, Jain, Vipul8, Viereck, Chris8, Castelli, Jeffrey P.8, Skuban, Nina8, Barth, Jay A.8, Bichet, Daniel G.9 |
| Source: | American Journal of Medical Genetics. Part A; Jun2019, Vol. 179 Issue 6, p1069-1073, 5p |
| Database: | Applied Science & Technology Source |
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