G.P.222 - Nonsense mutation dystrophinopathy: How mutation-specific treatments changed our clinical practice?

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Bibliographic Details
Title: G.P.222 - Nonsense mutation dystrophinopathy: How mutation-specific treatments changed our clinical practice?
Authors: Ardicli, D.1, Konuskan, B.1, Haliloglu, G.1, Alikasifoglu, M.1, Topaloğlu, H.1
Source: Neuromuscular Disorders. Oct2015 Supplement 2, Vol. 25, pS253-S253. 1p.
Database: Academic Search Ultimate
Description
ISSN:09608966
DOI:10.1016/j.nmd.2015.06.247