Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.
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| Title: | Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy. |
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| Authors: | Cox, Timothy M.1 tmc12@medschl.cam.ac.uk, Drelichman, Guillermo2, Cravo, Renata3, Balwani, Manisha4, Burrow, Thomas Andrew5, Martins, Ana Maria6, Lukina, Elena7, Rosenbloom, Barry8, Goker-Alpan, Ozlem9, Watman, Nora10, El-Beshlawy, Amal11, Kishnani, Priya S.12, Pedroso, Maria Lucia13, Gaemers, Sebastiaan J. M.14, Tayag, Regina15, Peterschmitt, M. Judith14 |
| Source: | Blood. 4/27/2017, Vol. 129 Issue 17, p2375-2383. 9p. 1 Diagram, 4 Charts, 2 Graphs. |
| Database: | Academic Search Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 122739299 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Cox%2C+Timothy+M%2E%22">Cox, Timothy M.</searchLink><relatesTo>1</relatesTo><i> tmc12@medschl.cam.ac.uk</i><br /><searchLink fieldCode="AR" term="%22Drelichman%2C+Guillermo%22">Drelichman, Guillermo</searchLink><relatesTo>2</relatesTo><br /><searchLink fieldCode="AR" term="%22Cravo%2C+Renata%22">Cravo, Renata</searchLink><relatesTo>3</relatesTo><br /><searchLink fieldCode="AR" term="%22Balwani%2C+Manisha%22">Balwani, Manisha</searchLink><relatesTo>4</relatesTo><br /><searchLink fieldCode="AR" term="%22Burrow%2C+Thomas+Andrew%22">Burrow, Thomas Andrew</searchLink><relatesTo>5</relatesTo><br /><searchLink fieldCode="AR" term="%22Martins%2C+Ana+Maria%22">Martins, Ana Maria</searchLink><relatesTo>6</relatesTo><br /><searchLink fieldCode="AR" term="%22Lukina%2C+Elena%22">Lukina, Elena</searchLink><relatesTo>7</relatesTo><br /><searchLink fieldCode="AR" term="%22Rosenbloom%2C+Barry%22">Rosenbloom, Barry</searchLink><relatesTo>8</relatesTo><br /><searchLink fieldCode="AR" term="%22Goker-Alpan%2C+Ozlem%22">Goker-Alpan, Ozlem</searchLink><relatesTo>9</relatesTo><br /><searchLink fieldCode="AR" term="%22Watman%2C+Nora%22">Watman, Nora</searchLink><relatesTo>10</relatesTo><br /><searchLink fieldCode="AR" term="%22El-Beshlawy%2C+Amal%22">El-Beshlawy, Amal</searchLink><relatesTo>11</relatesTo><br /><searchLink fieldCode="AR" term="%22Kishnani%2C+Priya+S%2E%22">Kishnani, Priya S.</searchLink><relatesTo>12</relatesTo><br /><searchLink fieldCode="AR" term="%22Pedroso%2C+Maria+Lucia%22">Pedroso, Maria Lucia</searchLink><relatesTo>13</relatesTo><br /><searchLink fieldCode="AR" term="%22Gaemers%2C+Sebastiaan+J%2E+M%2E%22">Gaemers, Sebastiaan J. M.</searchLink><relatesTo>14</relatesTo><br /><searchLink fieldCode="AR" term="%22Tayag%2C+Regina%22">Tayag, Regina</searchLink><relatesTo>15</relatesTo><br /><searchLink fieldCode="AR" term="%22Peterschmitt%2C+M%2E+Judith%22">Peterschmitt, M. Judith</searchLink><relatesTo>14</relatesTo> – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22Blood%22">Blood</searchLink>. 4/27/2017, Vol. 129 Issue 17, p2375-2383. 9p. 1 Diagram, 4 Charts, 2 Graphs. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=122739299 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1182/blood-2016-12-758409 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 9 StartPage: 2375 Titles: – TitleFull: Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Cox, Timothy M. – PersonEntity: Name: NameFull: Drelichman, Guillermo – PersonEntity: Name: NameFull: Cravo, Renata – PersonEntity: Name: NameFull: Balwani, Manisha – PersonEntity: Name: NameFull: Burrow, Thomas Andrew – PersonEntity: Name: NameFull: Martins, Ana Maria – PersonEntity: Name: NameFull: Lukina, Elena – PersonEntity: Name: NameFull: Rosenbloom, Barry – PersonEntity: Name: NameFull: Goker-Alpan, Ozlem – PersonEntity: Name: NameFull: Watman, Nora – PersonEntity: Name: NameFull: El-Beshlawy, Amal – PersonEntity: Name: NameFull: Kishnani, Priya S. – PersonEntity: Name: NameFull: Pedroso, Maria Lucia – PersonEntity: Name: NameFull: Gaemers, Sebastiaan J. M. – PersonEntity: Name: NameFull: Tayag, Regina – PersonEntity: Name: NameFull: Peterschmitt, M. Judith IsPartOfRelationships: – BibEntity: Dates: – D: 27 M: 04 Text: 4/27/2017 Type: published Y: 2017 Identifiers: – Type: issn-print Value: 00064971 Numbering: – Type: volume Value: 129 – Type: issue Value: 17 Titles: – TitleFull: Blood Type: main |
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