Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.

Saved in:
Bibliographic Details
Title: Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.
Authors: Cox, Timothy M.1 tmc12@medschl.cam.ac.uk, Drelichman, Guillermo2, Cravo, Renata3, Balwani, Manisha4, Burrow, Thomas Andrew5, Martins, Ana Maria6, Lukina, Elena7, Rosenbloom, Barry8, Goker-Alpan, Ozlem9, Watman, Nora10, El-Beshlawy, Amal11, Kishnani, Priya S.12, Pedroso, Maria Lucia13, Gaemers, Sebastiaan J. M.14, Tayag, Regina15, Peterschmitt, M. Judith14
Source: Blood. 4/27/2017, Vol. 129 Issue 17, p2375-2383. 9p. 1 Diagram, 4 Charts, 2 Graphs.
Database: Academic Search Ultimate
FullText Text:
  Availability: 0
Header DbId: asn
DbLabel: Academic Search Ultimate
An: 122739299
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AR" term="%22Cox%2C+Timothy+M%2E%22">Cox, Timothy M.</searchLink><relatesTo>1</relatesTo><i> tmc12@medschl.cam.ac.uk</i><br /><searchLink fieldCode="AR" term="%22Drelichman%2C+Guillermo%22">Drelichman, Guillermo</searchLink><relatesTo>2</relatesTo><br /><searchLink fieldCode="AR" term="%22Cravo%2C+Renata%22">Cravo, Renata</searchLink><relatesTo>3</relatesTo><br /><searchLink fieldCode="AR" term="%22Balwani%2C+Manisha%22">Balwani, Manisha</searchLink><relatesTo>4</relatesTo><br /><searchLink fieldCode="AR" term="%22Burrow%2C+Thomas+Andrew%22">Burrow, Thomas Andrew</searchLink><relatesTo>5</relatesTo><br /><searchLink fieldCode="AR" term="%22Martins%2C+Ana+Maria%22">Martins, Ana Maria</searchLink><relatesTo>6</relatesTo><br /><searchLink fieldCode="AR" term="%22Lukina%2C+Elena%22">Lukina, Elena</searchLink><relatesTo>7</relatesTo><br /><searchLink fieldCode="AR" term="%22Rosenbloom%2C+Barry%22">Rosenbloom, Barry</searchLink><relatesTo>8</relatesTo><br /><searchLink fieldCode="AR" term="%22Goker-Alpan%2C+Ozlem%22">Goker-Alpan, Ozlem</searchLink><relatesTo>9</relatesTo><br /><searchLink fieldCode="AR" term="%22Watman%2C+Nora%22">Watman, Nora</searchLink><relatesTo>10</relatesTo><br /><searchLink fieldCode="AR" term="%22El-Beshlawy%2C+Amal%22">El-Beshlawy, Amal</searchLink><relatesTo>11</relatesTo><br /><searchLink fieldCode="AR" term="%22Kishnani%2C+Priya+S%2E%22">Kishnani, Priya S.</searchLink><relatesTo>12</relatesTo><br /><searchLink fieldCode="AR" term="%22Pedroso%2C+Maria+Lucia%22">Pedroso, Maria Lucia</searchLink><relatesTo>13</relatesTo><br /><searchLink fieldCode="AR" term="%22Gaemers%2C+Sebastiaan+J%2E+M%2E%22">Gaemers, Sebastiaan J. M.</searchLink><relatesTo>14</relatesTo><br /><searchLink fieldCode="AR" term="%22Tayag%2C+Regina%22">Tayag, Regina</searchLink><relatesTo>15</relatesTo><br /><searchLink fieldCode="AR" term="%22Peterschmitt%2C+M%2E+Judith%22">Peterschmitt, M. Judith</searchLink><relatesTo>14</relatesTo>
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%22Blood%22">Blood</searchLink>. 4/27/2017, Vol. 129 Issue 17, p2375-2383. 9p. 1 Diagram, 4 Charts, 2 Graphs.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=122739299
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1182/blood-2016-12-758409
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        PageCount: 9
        StartPage: 2375
    Titles:
      – TitleFull: Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Cox, Timothy M.
      – PersonEntity:
          Name:
            NameFull: Drelichman, Guillermo
      – PersonEntity:
          Name:
            NameFull: Cravo, Renata
      – PersonEntity:
          Name:
            NameFull: Balwani, Manisha
      – PersonEntity:
          Name:
            NameFull: Burrow, Thomas Andrew
      – PersonEntity:
          Name:
            NameFull: Martins, Ana Maria
      – PersonEntity:
          Name:
            NameFull: Lukina, Elena
      – PersonEntity:
          Name:
            NameFull: Rosenbloom, Barry
      – PersonEntity:
          Name:
            NameFull: Goker-Alpan, Ozlem
      – PersonEntity:
          Name:
            NameFull: Watman, Nora
      – PersonEntity:
          Name:
            NameFull: El-Beshlawy, Amal
      – PersonEntity:
          Name:
            NameFull: Kishnani, Priya S.
      – PersonEntity:
          Name:
            NameFull: Pedroso, Maria Lucia
      – PersonEntity:
          Name:
            NameFull: Gaemers, Sebastiaan J. M.
      – PersonEntity:
          Name:
            NameFull: Tayag, Regina
      – PersonEntity:
          Name:
            NameFull: Peterschmitt, M. Judith
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 27
              M: 04
              Text: 4/27/2017
              Type: published
              Y: 2017
          Identifiers:
            – Type: issn-print
              Value: 00064971
          Numbering:
            – Type: volume
              Value: 129
            – Type: issue
              Value: 17
          Titles:
            – TitleFull: Blood
              Type: main
ResultId 1