TH.O.17 - Whole-body rescue of Pompe disease with AAV liver delivery of engineered secretable GAA transgenes.
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| Title: | TH.O.17 - Whole-body rescue of Pompe disease with AAV liver delivery of engineered secretable GAA transgenes. |
|---|---|
| Authors: | Colella, P.1, Puzzo, F.1, Biferi, M.2, Bali, D.3, Paulk, N.4, Vidal, P.1, Collaud, F.1, Simon-Sola, M.1, Charles, S.1, Hardet, R.2, Leborgne, C.1, Sellier, P.1, Van Wittenberghe, L.1, Boisgerault, F.1, Barkats, M.2, Laforêt, P.5, Kay, M.4, Koeberl, D.3, Ronzitti, G.1, Mingozzi, F.6 |
| Source: | Neuromuscular Disorders. Oct2017 Supplement 2, Vol. 27, pS246-S246. 1p. |
| Database: | Academic Search Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 125081586 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=125081586 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.nmd.2017.06.543 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 1 StartPage: S246 Titles: – TitleFull: TH.O.17 - Whole-body rescue of Pompe disease with AAV liver delivery of engineered secretable GAA transgenes. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Colella, P. – PersonEntity: Name: NameFull: Puzzo, F. – PersonEntity: Name: NameFull: Biferi, M. – PersonEntity: Name: NameFull: Bali, D. – PersonEntity: Name: NameFull: Paulk, N. – PersonEntity: Name: NameFull: Vidal, P. – PersonEntity: Name: NameFull: Collaud, F. – PersonEntity: Name: NameFull: Simon-Sola, M. – PersonEntity: Name: NameFull: Charles, S. – PersonEntity: Name: NameFull: Hardet, R. – PersonEntity: Name: NameFull: Leborgne, C. – PersonEntity: Name: NameFull: Sellier, P. – PersonEntity: Name: NameFull: Van Wittenberghe, L. – PersonEntity: Name: NameFull: Boisgerault, F. – PersonEntity: Name: NameFull: Barkats, M. – PersonEntity: Name: NameFull: Laforêt, P. – PersonEntity: Name: NameFull: Kay, M. – PersonEntity: Name: NameFull: Koeberl, D. – PersonEntity: Name: NameFull: Ronzitti, G. – PersonEntity: Name: NameFull: Mingozzi, F. IsPartOfRelationships: – BibEntity: Dates: – D: 02 M: 10 Text: Oct2017 Supplement 2 Type: published Y: 2017 Identifiers: – Type: issn-print Value: 09608966 Numbering: – Type: volume Value: 27 Titles: – TitleFull: Neuromuscular Disorders Type: main |
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