Assessing Preferences for Rare Disease Treatment: Qualitative Development of the Paroxysmal Nocturnal Hemoglobinuria Patient Preference Questionnaire (PNH-PPQ©). - Kaiser, Karen; Yount, Susan E; Martens, Christa E; Webster, Kimberly A; Shaunfield, Sara; Sparling, Amy; Peipert, John Devin; Cella, David; Rottinghaus, Scott T; Donato, Bonnie MK; Wells, Richard; Tomazos, Ioannis (Patient Preference & Adherence, 2020)