Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus.
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| Title: | Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus. |
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| Authors: | Moreno-Martinez, D.1 (AUTHOR), Aguiar, P.2 (AUTHOR), Auray-Blais, C.3 (AUTHOR), Beck, M.4 (AUTHOR), Bichet, D.G.5 (AUTHOR), Burlina, A.6 (AUTHOR), Cole, D.7 (AUTHOR), Elliott, P.8 (AUTHOR), Feldt-Rasmussen, U.9 (AUTHOR), Feriozzi, S.10 (AUTHOR), Fletcher, J.11 (AUTHOR), Giugliani, R.12 (AUTHOR), Jovanovic, A.13 (AUTHOR), Kampmann, C.14 (AUTHOR), Langeveld, M.15 (AUTHOR), Lidove, O.16 (AUTHOR), Linhart, A.17 (AUTHOR), Mauer, M.18 (AUTHOR), Moon, J.C.19 (AUTHOR), Muir, A.20 (AUTHOR) |
| Source: | Molecular Genetics & Metabolism. Apr2021, Vol. 132 Issue 4, p234-243. 10p. |
| Database: | Academic Search Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 149368263 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=149368263 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.ymgme.2021.02.001 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 10 StartPage: 234 Titles: – TitleFull: Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Moreno-Martinez, D. – PersonEntity: Name: NameFull: Aguiar, P. – PersonEntity: Name: NameFull: Auray-Blais, C. – PersonEntity: Name: NameFull: Beck, M. – PersonEntity: Name: NameFull: Bichet, D.G. – PersonEntity: Name: NameFull: Burlina, A. – PersonEntity: Name: NameFull: Cole, D. – PersonEntity: Name: NameFull: Elliott, P. – PersonEntity: Name: NameFull: Feldt-Rasmussen, U. – PersonEntity: Name: NameFull: Feriozzi, S. – PersonEntity: Name: NameFull: Fletcher, J. – PersonEntity: Name: NameFull: Giugliani, R. – PersonEntity: Name: NameFull: Jovanovic, A. – PersonEntity: Name: NameFull: Kampmann, C. – PersonEntity: Name: NameFull: Langeveld, M. – PersonEntity: Name: NameFull: Lidove, O. – PersonEntity: Name: NameFull: Linhart, A. – PersonEntity: Name: NameFull: Mauer, M. – PersonEntity: Name: NameFull: Moon, J.C. – PersonEntity: Name: NameFull: Muir, A. IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 04 Text: Apr2021 Type: published Y: 2021 Identifiers: – Type: issn-print Value: 10967192 Numbering: – Type: volume Value: 132 – Type: issue Value: 4 Titles: – TitleFull: Molecular Genetics & Metabolism Type: main |
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