Presymptomatic treatment of classic late-infantile neuronal ceroid lipofuscinosis with cerliponase alfa.
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| Title: | Presymptomatic treatment of classic late-infantile neuronal ceroid lipofuscinosis with cerliponase alfa. |
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| Authors: | Schaefers, J.1 (AUTHOR), van der Giessen, L. J.2 (AUTHOR), Klees, C.3 (AUTHOR), Jacobs, E. H.4 (AUTHOR), Sieverdink, S.1 (AUTHOR), Dremmen, M. H. G.5 (AUTHOR), Spoor, J. K. H.6 (AUTHOR), van der Ploeg, A. T.1 (AUTHOR), van den Hout, J. M. P.1 (AUTHOR), Huidekoper, H. H.1 (AUTHOR) h.huidekoper@erasmusmc.nl |
| Source: | Orphanet Journal of Rare Diseases. 5/14/2021, Vol. 16 Issue 1, p1-9. 9p. |
| Database: | Academic Search Ultimate |
| ISSN: | 17501172 |
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| DOI: | 10.1186/s13023-021-01858-6 |
