Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor.
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| Title: | Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor. |
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| Authors: | Babcock, Michael C.1, Mikulka, Christina R.2, Wang, Bing1, Chandriani, Sanjay1, Chandra, Sundeep1, Xu, Yue1, Webster, Katherine1, Feng, Ying1, Nelvagal, Hemanth R.3, Giaramita, Alex1, Yip, Bryan K.1, Lo, Melanie1, Jiang, Xuntian2, Chao, Qi1, Woloszynek, Josh C.1, Shen, Yuqiao1, Bhagwat, Shripad1, Sands, Mark S.2,4, Crawford, Brett E.1 bcrawford@bmrn.com |
| Source: | Scientific Reports. 7/14/2021, Vol. 11 Issue 1, p1-17. 17p. |
| Database: | Academic Search Ultimate |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 151401467 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=151401467 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1038/s41598-021-93601-1 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 17 StartPage: 1 Titles: – TitleFull: Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Babcock, Michael C. – PersonEntity: Name: NameFull: Mikulka, Christina R. – PersonEntity: Name: NameFull: Wang, Bing – PersonEntity: Name: NameFull: Chandriani, Sanjay – PersonEntity: Name: NameFull: Chandra, Sundeep – PersonEntity: Name: NameFull: Xu, Yue – PersonEntity: Name: NameFull: Webster, Katherine – PersonEntity: Name: NameFull: Feng, Ying – PersonEntity: Name: NameFull: Nelvagal, Hemanth R. – PersonEntity: Name: NameFull: Giaramita, Alex – PersonEntity: Name: NameFull: Yip, Bryan K. – PersonEntity: Name: NameFull: Lo, Melanie – PersonEntity: Name: NameFull: Jiang, Xuntian – PersonEntity: Name: NameFull: Chao, Qi – PersonEntity: Name: NameFull: Woloszynek, Josh C. – PersonEntity: Name: NameFull: Shen, Yuqiao – PersonEntity: Name: NameFull: Bhagwat, Shripad – PersonEntity: Name: NameFull: Sands, Mark S. – PersonEntity: Name: NameFull: Crawford, Brett E. IsPartOfRelationships: – BibEntity: Dates: – D: 14 M: 07 Text: 7/14/2021 Type: published Y: 2021 Identifiers: – Type: issn-print Value: 20452322 Numbering: – Type: volume Value: 11 – Type: issue Value: 1 Titles: – TitleFull: Scientific Reports Type: main |
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