DMD - TREATMENT: EP.146 scAAV.U7snRNA-mediated therapy: prolonged dystrophin expression and muscle function correction in adult Dup2 mice.
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| Title: | DMD - TREATMENT: EP.146 scAAV.U7snRNA-mediated therapy: prolonged dystrophin expression and muscle function correction in adult Dup2 mice. |
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| Authors: | Gushchina, L.1 (AUTHOR), Bradley, A.1 (AUTHOR), Vetter, T.1 (AUTHOR), Frair, E.1 (AUTHOR), Bellinger, C.1 (AUTHOR), Simmons, T.1 (AUTHOR), Rohan, N.1 (AUTHOR), Wein, N.1 (AUTHOR), Flanigan, K.1 (AUTHOR) |
| Source: | Neuromuscular Disorders. 2021 Supplement 1, Vol. 31, pS93-S93. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 09608966 |
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| DOI: | 10.1016/j.nmd.2021.07.171 |