Long-term effectiveness of carglumic acid in patients with propionic acidemia (PA) and methylmalonic acidemia (MMA): a randomized clinical trial.

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Title: Long-term effectiveness of carglumic acid in patients with propionic acidemia (PA) and methylmalonic acidemia (MMA): a randomized clinical trial.
Authors: Alfadhel, Majid1 (AUTHOR) dralfadhelm@gmail.com, Nashabat, Marwan1 (AUTHOR), Saleh, Mohammed2 (AUTHOR), Elamin, Mohammed2 (AUTHOR), Alfares, Ahmed3 (AUTHOR), Al Othaim, Ali4 (AUTHOR), Umair, Muhammad5 (AUTHOR), Ahmed, Hind1 (AUTHOR), Ababneh, Faroug1 (AUTHOR), Al Mutairi, Fuad1 (AUTHOR), Eyaid, Wafaa1 (AUTHOR), Alswaid, Abdulrahman1 (AUTHOR), Alohali, Lina1 (AUTHOR), Faqeih, Eissa2 (AUTHOR), Almannai, Mohammed2 (AUTHOR), Aljeraisy, Majed6 (AUTHOR), Albdah, Bayan7 (AUTHOR), Hussein, Mohamed A.7 (AUTHOR), Rahbeeni, Zuhair8 (AUTHOR), Alasmari, Ali2 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 10/11/2021, Vol. 16 Issue 1, p1-10. 10p.
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  Data: Long-term effectiveness of carglumic acid in patients with propionic acidemia (PA) and methylmalonic acidemia (MMA): a randomized clinical trial.
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 10/11/2021, Vol. 16 Issue 1, p1-10. 10p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=152947878
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              Text: 10/11/2021
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