Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice - Liu, Yuli; Xu, Lingfei; Hennig, Anne K.; Kovacs, Attila; Fu, Annabel; Chung, Sarah; Lee, David; Wang, Bin; Herati, Ramin S.; Mosinger Ogilvie, Judith; Cai, Shi-Rong; Parker Ponder, Katherine (Molecular Therapy, 2005)