Genomic landscape of lymphatic malformations: a case series and response to the PI3Ka inhibitor alpelisib in an N-of-1 clinical trial.

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Title: Genomic landscape of lymphatic malformations: a case series and response to the PI3Ka inhibitor alpelisib in an N-of-1 clinical trial.
Authors: Shaheen, Montaser F.1,2 shaheenm@arizona.edu, Tse, Julie Y.3, Sokol, Ethan S.3, Masterson, Margaret4,5, Bansal, Pranshu6, Rabinowitz, Ian6,7, Tarleton, Christy A.6, Dobroff, Andrey S.6,8, Smith, Tracey L.9,10, Bocklage, Thèrése J.6,11, Mannakee, Brian K.1,12, Gutenkunst, Ryan N.1,13, Bischoff, Joyce14,15, Ness, Scott A.6,8, Riedlinger, Gregory M.4,16, Groisberg, Roman4,17, Pasqualini, Renata9,10, Ganesan, Shridar4 ganesash@cinj.rutgers.edu, Arap, Wadih9,18 wadih.arap@rutgers.edu
Source: eLife. 7/5/2022, p1-17. 17p.
Database: Academic Search Ultimate
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PubType: Academic Journal
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