Stakeholders' views on drug development: the congenital disorders of glycosylation community perspective. - Monticelli, Maria; Francisco, Rita; Brasil, Sandra; Marques-da-Silva, Dorinda; Rijoff, Tatiana; Pascoal, Carlota; Jaeken, Jaak; Videira, Paula A.; dos Reis Ferreira, Vanessa (Orphanet Journal of Rare Diseases, 2022)