P.65 Consistency of changes in percent-predicted forced vital capacity between real-world data and trial placebo arms in ambulatory Duchenne muscular dystrophy.
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| Title: | P.65 Consistency of changes in percent-predicted forced vital capacity between real-world data and trial placebo arms in ambulatory Duchenne muscular dystrophy. |
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| Authors: | Goemans, N.1 (AUTHOR), McDonald, C.2 (AUTHOR), Muntoni, F.3 (AUTHOR), Signorovitch, J.4 (AUTHOR), Sajeev, G.4 (AUTHOR), Done, N.4 (AUTHOR), Manzur, A.3 (AUTHOR), Wong, B.5 (AUTHOR), Tian, C.6 (AUTHOR), Mercuri, E.7 (AUTHOR), He, C.4 (AUTHOR), Peterson, D.4 (AUTHOR), Akbarnejad, H.4 (AUTHOR), Ward, S.8 (AUTHOR) |
| Source: | Neuromuscular Disorders. 2022 Supplement 1, Vol. 32, pS68-S69. 2p. |
| Database: | Academic Search Ultimate |
| ISSN: | 09608966 |
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| DOI: | 10.1016/j.nmd.2022.07.113 |