Efficacy and pharmacokinetics of betaine in CBS and cblC deficiencies: a cross-over randomized controlled trial.

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Title: Efficacy and pharmacokinetics of betaine in CBS and cblC deficiencies: a cross-over randomized controlled trial.
Authors: Imbard, Apolline1,2,3 (AUTHOR) apolline.imbard@aphp.fr, Toumazi, Artemis4,5 (AUTHOR), Magréault, Sophie6,7 (AUTHOR), Garcia-Segarra, Nuria8,9 (AUTHOR), Schlemmer, Dimitri1 (AUTHOR), Kaguelidou, Florentia5,10 (AUTHOR), Perronneau, Isabelle1 (AUTHOR), Haignere, Jérémie4 (AUTHOR), de Baulny, Hélène Ogier8 (AUTHOR), Kuster, Alice11 (AUTHOR), Feillet, François12 (AUTHOR), Alberti, Corinne4 (AUTHOR), Guilmin-Crépon, Sophie4,5 (AUTHOR), Benoist, Jean-François1,2,3 (AUTHOR), Schiff, Manuel8,13,14 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 11/14/2022, Vol. 17 Issue 1, p1-13. 13p.
Database: Academic Search Ultimate
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An: 160201503
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  Data: Efficacy and pharmacokinetics of betaine in CBS and cblC deficiencies: a cross-over randomized controlled trial.
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 11/14/2022, Vol. 17 Issue 1, p1-13. 13p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=160201503
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        Value: 10.1186/s13023-022-02567-4
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        Text: English
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              Text: 11/14/2022
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