Quality of life improvements following one year of setmelanotide in children and adult patients with Bardet–Biedl syndrome: phase 3 trial results. - Forsythe, Elizabeth; Haws, Robert M.; Argente, Jesús; Beales, Philip; Martos-Moreno, Gabriel Á.; Dollfus, Hélène; Chirila, Costel; Gnanasakthy, Ari; Buckley, Brieana C.; Mallya, Usha G.; Clément, Karine; Haqq, Andrea M. (Orphanet Journal of Rare Diseases, 2023)