Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.
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| Title: | Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment. |
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| Authors: | Symington, Emily1 (AUTHOR) emily.symington1@nhs.net, Rangarajan, Savita2 (AUTHOR), Lester, Will3 (AUTHOR), Madan, Bella4 (AUTHOR), Pierce, Glenn F.5 (AUTHOR), Raheja, Priyanka6 (AUTHOR), Robinson, Tara M.7 (AUTHOR), Osmond, Dane7 (AUTHOR), Russell, Chris B.7 (AUTHOR), Vettermann, Christian7 (AUTHOR), Agarwal, Suresh K.7 (AUTHOR), Li, Mingjin7 (AUTHOR), Wong, Wing Yen7 (AUTHOR), Laffan, Michael8 (AUTHOR) |
| Source: | Haemophilia. Mar2024, Vol. 30 Issue 2, p320-330. 11p. |
| Database: | Academic Search Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 175988680 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Symington%2C+Emily%22">Symington, Emily</searchLink><relatesTo>1</relatesTo> (AUTHOR)<i> emily.symington1@nhs.net</i><br /><searchLink fieldCode="AR" term="%22Rangarajan%2C+Savita%22">Rangarajan, Savita</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Lester%2C+Will%22">Lester, Will</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Madan%2C+Bella%22">Madan, Bella</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Pierce%2C+Glenn+F%2E%22">Pierce, Glenn F.</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Raheja%2C+Priyanka%22">Raheja, Priyanka</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Robinson%2C+Tara+M%2E%22">Robinson, Tara M.</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Osmond%2C+Dane%22">Osmond, Dane</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Russell%2C+Chris+B%2E%22">Russell, Chris B.</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Vettermann%2C+Christian%22">Vettermann, Christian</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Agarwal%2C+Suresh+K%2E%22">Agarwal, Suresh K.</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Li%2C+Mingjin%22">Li, Mingjin</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Wong%2C+Wing+Yen%22">Wong, Wing Yen</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Laffan%2C+Michael%22">Laffan, Michael</searchLink><relatesTo>8</relatesTo> (AUTHOR) – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22Haemophilia%22">Haemophilia</searchLink>. Mar2024, Vol. 30 Issue 2, p320-330. 11p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=175988680 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1111/hae.14936 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 11 StartPage: 320 Titles: – TitleFull: Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Symington, Emily – PersonEntity: Name: NameFull: Rangarajan, Savita – PersonEntity: Name: NameFull: Lester, Will – PersonEntity: Name: NameFull: Madan, Bella – PersonEntity: Name: NameFull: Pierce, Glenn F. – PersonEntity: Name: NameFull: Raheja, Priyanka – PersonEntity: Name: NameFull: Robinson, Tara M. – PersonEntity: Name: NameFull: Osmond, Dane – PersonEntity: Name: NameFull: Russell, Chris B. – PersonEntity: Name: NameFull: Vettermann, Christian – PersonEntity: Name: NameFull: Agarwal, Suresh K. – PersonEntity: Name: NameFull: Li, Mingjin – PersonEntity: Name: NameFull: Wong, Wing Yen – PersonEntity: Name: NameFull: Laffan, Michael IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 03 Text: Mar2024 Type: published Y: 2024 Identifiers: – Type: issn-print Value: 13518216 Numbering: – Type: volume Value: 30 – Type: issue Value: 2 Titles: – TitleFull: Haemophilia Type: main |
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