Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.

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Title: Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.
Authors: Symington, Emily1 (AUTHOR) emily.symington1@nhs.net, Rangarajan, Savita2 (AUTHOR), Lester, Will3 (AUTHOR), Madan, Bella4 (AUTHOR), Pierce, Glenn F.5 (AUTHOR), Raheja, Priyanka6 (AUTHOR), Robinson, Tara M.7 (AUTHOR), Osmond, Dane7 (AUTHOR), Russell, Chris B.7 (AUTHOR), Vettermann, Christian7 (AUTHOR), Agarwal, Suresh K.7 (AUTHOR), Li, Mingjin7 (AUTHOR), Wong, Wing Yen7 (AUTHOR), Laffan, Michael8 (AUTHOR)
Source: Haemophilia. Mar2024, Vol. 30 Issue 2, p320-330. 11p.
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  Data: Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.
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  Data: <searchLink fieldCode="JN" term="%22Haemophilia%22">Haemophilia</searchLink>. Mar2024, Vol. 30 Issue 2, p320-330. 11p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=175988680
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      – Type: doi
        Value: 10.1111/hae.14936
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      – Code: eng
        Text: English
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        PageCount: 11
        StartPage: 320
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      – TitleFull: Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.
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              Text: Mar2024
              Type: published
              Y: 2024
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