Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.
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| Title: | Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment. |
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| Authors: | Symington, Emily1 (AUTHOR) emily.symington1@nhs.net, Rangarajan, Savita2 (AUTHOR), Lester, Will3 (AUTHOR), Madan, Bella4 (AUTHOR), Pierce, Glenn F.5 (AUTHOR), Raheja, Priyanka6 (AUTHOR), Robinson, Tara M.7 (AUTHOR), Osmond, Dane7 (AUTHOR), Russell, Chris B.7 (AUTHOR), Vettermann, Christian7 (AUTHOR), Agarwal, Suresh K.7 (AUTHOR), Li, Mingjin7 (AUTHOR), Wong, Wing Yen7 (AUTHOR), Laffan, Michael8 (AUTHOR) |
| Source: | Haemophilia. Mar2024, Vol. 30 Issue 2, p320-330. 11p. |
| Database: | Academic Search Ultimate |
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