A 360-degree perspective on adeno-associated virus (AAV)-based gene therapy for haemophilia: Insights from the physician, the nurse and the patient. - Miesbach, Wolfgang; Mulders, Greta; Breederveld, Daan; Pinachyan, Karen; Le Quellec, Sandra; Pabinger, Ingrid (Orphanet Journal of Rare Diseases, 2024)