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Twice weekly dosing with Sebelipase alfa (Kanuma®) rescues severely ill infants with Wolman disease.

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Title: Twice weekly dosing with Sebelipase alfa (Kanuma®) rescues severely ill infants with Wolman disease.
Authors: de Castro, María José1,2 (AUTHOR), Jones, Simon A3,4 (AUTHOR) simonallanjones@gmail.com, de las Heras, Javier5 (AUTHOR), Sánchez-Pintos, Paula1,2 (AUTHOR), Couce, María L1,2 (AUTHOR), Colón, Cristóbal1,2 (AUTHOR), Crujeiras, Pablo1,2 (AUTHOR), Unceta, María5 (AUTHOR), Church, Heather3 (AUTHOR), Brammeier, Kathryn3 (AUTHOR), Yee, Wu Hoi3 (AUTHOR), Cooper, James3 (AUTHOR), López de Frutos, Laura6 (AUTHOR), Serrano-Gonzalo, Irene6 (AUTHOR), Camba, María José1,2 (AUTHOR), White, Fiona J.3 (AUTHOR), Holmes, Victoria3 (AUTHOR), Ghosh, Arunabha3,4 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 6/25/2024, Vol. 19 Issue 1, p1-9. 9p.
Database: Academic Search Ultimate
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  Data: Twice weekly dosing with Sebelipase alfa (Kanuma®) rescues severely ill infants with Wolman disease.
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 6/25/2024, Vol. 19 Issue 1, p1-9. 9p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=178085845
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              M: 06
              Text: 6/25/2024
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              Y: 2024
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