A rare partnership: patient community and industry collaboration to shape the impact of real-world evidence on the rare disease ecosystem. - Klein, T. L.; Bender, J.; Bolton, S.; Collin-Histed, T.; Daher, A.; De Baere, L.; Dong, D.; Hopkin, J.; Johnson, J.; Lai, T.; Pavlou, M.; Schaller, T.; et al. (Orphanet Journal of Rare Diseases, 2024)