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Review of clinical trials and guidelines for children and youth with mucopolysaccharidosis: outcome selection and measurement.

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Title: Review of clinical trials and guidelines for children and youth with mucopolysaccharidosis: outcome selection and measurement.
Authors: Howie, Alison H.1 (AUTHOR), Tingley, Kylie1 (AUTHOR), Inbar-Feigenberg, Michal2 (AUTHOR), Mitchell, John J.3 (AUTHOR), Angel, Kim4 (AUTHOR), Gentle, Jenifer5 (AUTHOR), Smith, Maureen6 (AUTHOR), Offringa, Martin7 (AUTHOR), Butcher, Nancy J.8 (AUTHOR), Campeau, Philippe M.9 (AUTHOR), Chakraborty, Pranesh10 (AUTHOR), Chan, Alicia11 (AUTHOR), Fergusson, Dean12 (AUTHOR), Mamak, Eva13 (AUTHOR), McClelland, Peyton10 (AUTHOR), Mercimek-Andrews, Saadet11 (AUTHOR), Mhanni, Aizeddin14,15 (AUTHOR), Moazin, Zeinab10 (AUTHOR), Rockman-Greenberg, Cheryl15 (AUTHOR), Rupar, C. Anthony16 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 10/23/2024, Vol. 19 Issue 1, p1-15. 15p.
Database: Academic Search Ultimate
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PubType: Academic Journal
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 10/23/2024, Vol. 19 Issue 1, p1-15. 15p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=180457914
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              Text: 10/23/2024
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