Genotype-specific effects of elamipretide in patients with primary mitochondrial myopathy: a post hoc analysis of the MMPOWER-3 trial.

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Title: Genotype-specific effects of elamipretide in patients with primary mitochondrial myopathy: a post hoc analysis of the MMPOWER-3 trial.
Authors: Karaa, Amel1 (AUTHOR) AKARAA@mgh.harvard.edu, Bertini, Enrico2 (AUTHOR), Carelli, Valerio3,4 (AUTHOR), Cohen, Bruce5 (AUTHOR), Ennes, Gregory M.6 (AUTHOR), Falk, Marni J.7 (AUTHOR), Goldstein, Amy7 (AUTHOR), Gorman, Gráinne8 (AUTHOR), Haas, Richard9 (AUTHOR), Hirano, Michio10 (AUTHOR), Klopstock, Thomas11,12,13 (AUTHOR), Koenig, Mary Kay14 (AUTHOR), Kornblum, Cornelia15 (AUTHOR), Lamperti, Costanza16 (AUTHOR), Lehman, Anna17 (AUTHOR), Longo, Nicola18 (AUTHOR), Molnar, Maria Judit19 (AUTHOR), Parikh, Sumit20 (AUTHOR), Phan, Han21 (AUTHOR), Pitceathly, Robert D. S.22,23 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 11/21/2024, Vol. 19 Issue 1, p1-12. 12p.
Database: Academic Search Ultimate
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ISSN:17501172
DOI:10.1186/s13023-024-03421-5