Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement.

Saved in:
Bibliographic Details
Title: Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement.
Authors: Giugliani, Roberto1,2 (AUTHOR) rgiugliani@hcpa.edu.br, de Siqueira, Ana Cecília Menezes3 (AUTHOR), Santos, Emerson Santana4 (AUTHOR), Leão, Emília Katiane E. A.5 (AUTHOR), Carvalho, Gerson da Silva6 (AUTHOR), Santos, Mara Lúcia Schmitz Ferreira7 (AUTHOR), Raskin, Salmo8 (AUTHOR), Martins, Ana Maria9 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 11/26/2024, Vol. 19 Issue 1, p1-6. 6p.
Database: Academic Search Ultimate
Full text is not displayed to guests.
FullText Links:
  – Type: pdflink
Text:
  Availability: 1
Header DbId: asn
DbLabel: Academic Search Ultimate
An: 181133452
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AR" term="%22Giugliani%2C+Roberto%22">Giugliani, Roberto</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<i> rgiugliani@hcpa.edu.br</i><br /><searchLink fieldCode="AR" term="%22de+Siqueira%2C+Ana+Cecília+Menezes%22">de Siqueira, Ana Cecília Menezes</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Santos%2C+Emerson+Santana%22">Santos, Emerson Santana</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Leão%2C+Emília+Katiane+E%2E+A%2E%22">Leão, Emília Katiane E. A.</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Carvalho%2C+Gerson+da+Silva%22">Carvalho, Gerson da Silva</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Santos%2C+Mara+Lúcia+Schmitz+Ferreira%22">Santos, Mara Lúcia Schmitz Ferreira</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Raskin%2C+Salmo%22">Raskin, Salmo</searchLink><relatesTo>8</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Martins%2C+Ana+Maria%22">Martins, Ana Maria</searchLink><relatesTo>9</relatesTo> (AUTHOR)
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 11/26/2024, Vol. 19 Issue 1, p1-6. 6p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=181133452
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1186/s13023-024-03463-9
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        PageCount: 6
        StartPage: 1
    Titles:
      – TitleFull: Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Giugliani, Roberto
      – PersonEntity:
          Name:
            NameFull: de Siqueira, Ana Cecília Menezes
      – PersonEntity:
          Name:
            NameFull: Santos, Emerson Santana
      – PersonEntity:
          Name:
            NameFull: Leão, Emília Katiane E. A.
      – PersonEntity:
          Name:
            NameFull: Carvalho, Gerson da Silva
      – PersonEntity:
          Name:
            NameFull: Santos, Mara Lúcia Schmitz Ferreira
      – PersonEntity:
          Name:
            NameFull: Raskin, Salmo
      – PersonEntity:
          Name:
            NameFull: Martins, Ana Maria
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 26
              M: 11
              Text: 11/26/2024
              Type: published
              Y: 2024
          Identifiers:
            – Type: issn-print
              Value: 17501172
          Numbering:
            – Type: volume
              Value: 19
            – Type: issue
              Value: 1
          Titles:
            – TitleFull: Orphanet Journal of Rare Diseases
              Type: main
ResultId 1