Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement.
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| Title: | Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement. |
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| Authors: | Giugliani, Roberto1,2 (AUTHOR) rgiugliani@hcpa.edu.br, de Siqueira, Ana Cecília Menezes3 (AUTHOR), Santos, Emerson Santana4 (AUTHOR), Leão, Emília Katiane E. A.5 (AUTHOR), Carvalho, Gerson da Silva6 (AUTHOR), Santos, Mara Lúcia Schmitz Ferreira7 (AUTHOR), Raskin, Salmo8 (AUTHOR), Martins, Ana Maria9 (AUTHOR) |
| Source: | Orphanet Journal of Rare Diseases. 11/26/2024, Vol. 19 Issue 1, p1-6. 6p. |
| Database: | Academic Search Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 181133452 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Giugliani%2C+Roberto%22">Giugliani, Roberto</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<i> rgiugliani@hcpa.edu.br</i><br /><searchLink fieldCode="AR" term="%22de+Siqueira%2C+Ana+Cecília+Menezes%22">de Siqueira, Ana Cecília Menezes</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Santos%2C+Emerson+Santana%22">Santos, Emerson Santana</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Leão%2C+Emília+Katiane+E%2E+A%2E%22">Leão, Emília Katiane E. A.</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Carvalho%2C+Gerson+da+Silva%22">Carvalho, Gerson da Silva</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Santos%2C+Mara+Lúcia+Schmitz+Ferreira%22">Santos, Mara Lúcia Schmitz Ferreira</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Raskin%2C+Salmo%22">Raskin, Salmo</searchLink><relatesTo>8</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Martins%2C+Ana+Maria%22">Martins, Ana Maria</searchLink><relatesTo>9</relatesTo> (AUTHOR) – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 11/26/2024, Vol. 19 Issue 1, p1-6. 6p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=181133452 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1186/s13023-024-03463-9 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 6 StartPage: 1 Titles: – TitleFull: Heparan sulfate in cerebrospinal fluid as a biomarker to assess disease severity and for treatment monitoring in patients with Mucopolysaccharidosis Type II: a position statement. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Giugliani, Roberto – PersonEntity: Name: NameFull: de Siqueira, Ana Cecília Menezes – PersonEntity: Name: NameFull: Santos, Emerson Santana – PersonEntity: Name: NameFull: Leão, Emília Katiane E. A. – PersonEntity: Name: NameFull: Carvalho, Gerson da Silva – PersonEntity: Name: NameFull: Santos, Mara Lúcia Schmitz Ferreira – PersonEntity: Name: NameFull: Raskin, Salmo – PersonEntity: Name: NameFull: Martins, Ana Maria IsPartOfRelationships: – BibEntity: Dates: – D: 26 M: 11 Text: 11/26/2024 Type: published Y: 2024 Identifiers: – Type: issn-print Value: 17501172 Numbering: – Type: volume Value: 19 – Type: issue Value: 1 Titles: – TitleFull: Orphanet Journal of Rare Diseases Type: main |
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