Golodirsen restores DMD transcript imbalance in Duchenne Muscular Dystrophy patient muscle cells.
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| Title: | Golodirsen restores DMD transcript imbalance in Duchenne Muscular Dystrophy patient muscle cells. |
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| Authors: | Rossi, Rachele1,2 (AUTHOR), Torelli, Silvia1,2 (AUTHOR), Moore, Marc1,2,3 (AUTHOR), Ala, Pierpaolo1,2 (AUTHOR), Morgan, Jennifer1,2 (AUTHOR), Malhotra, Jyoti4 (AUTHOR), Muntoni, Francesco1,2 (AUTHOR) f.muntoni@ucl.ac.uk |
| Source: | Skeletal Muscle. 11/29/2024, Vol. 14 Issue 1, p1-14. 14p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20445040 |
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| DOI: | 10.1186/s13395-024-00360-4 |