Methodological insights from the EPISTOP trial to designing clinical trials in rare diseases—A secondary analysis of a randomized clinical trial. - Wied, Stephanie; Hilgers, Ralf-Dieter; Heussen, Nicole; Kotulska, Katarzyna; Dirani, Maya; Kuchenbuch, Mathieu; Jozwiak, Sergiusz; Nabbout, Rima (PLoS ONE, 2024)