Plasmid Gene Therapy for Monogenic Disorders: Challenges and Perspectives.

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Title: Plasmid Gene Therapy for Monogenic Disorders: Challenges and Perspectives.
Authors: Luís, Marco A.1,2,3 (AUTHOR) marco.luis@ubi.pt, Goes, Marcelo A. D.1,2,3 (AUTHOR) marcelo.goes@ubi.pt, Santos, Fátima Milhano1,2,4 (AUTHOR) fatima.milhano@quironsalud.es, Mesquita, Joana1,2 (AUTHOR) joana.mesquita@ubi.pt, Tavares-Ratado, Paulo1,5,6 (AUTHOR) ptavares@fcsaude.ubi.pt, Tomaz, Cândida Teixeira1,2,3 (AUTHOR) ctomaz@ubi.pt
Source: Pharmaceutics. Jan2025, Vol. 17 Issue 1, p104. 28p.
Database: Academic Search Ultimate
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ISSN:19994923
DOI:10.3390/pharmaceutics17010104