Plasmid Gene Therapy for Monogenic Disorders: Challenges and Perspectives.
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| Title: | Plasmid Gene Therapy for Monogenic Disorders: Challenges and Perspectives. |
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| Authors: | Luís, Marco A.1,2,3 (AUTHOR) marco.luis@ubi.pt, Goes, Marcelo A. D.1,2,3 (AUTHOR) marcelo.goes@ubi.pt, Santos, Fátima Milhano1,2,4 (AUTHOR) fatima.milhano@quironsalud.es, Mesquita, Joana1,2 (AUTHOR) joana.mesquita@ubi.pt, Tavares-Ratado, Paulo1,5,6 (AUTHOR) ptavares@fcsaude.ubi.pt, Tomaz, Cândida Teixeira1,2,3 (AUTHOR) ctomaz@ubi.pt |
| Source: | Pharmaceutics. Jan2025, Vol. 17 Issue 1, p104. 28p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 19994923 |
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| DOI: | 10.3390/pharmaceutics17010104 |