Clinically meaningful improvements after gene therapy for aromatic L-amino acid decarboxylase deficiency (AADCd) in the Peabody Developmental Motor Scale, Second Edition (PDMS-2) and correlation with Bayley-III scores and motor milestones. - Hwu, Wuh-Liang; Lee, Hui-Min; Peipert, John Devin; Zhang, Rongrong; Werner, Christian; Sierra, J. Rafael; O'Connell, Thomas; Woolley, Jonathan J.; Crowell, Marjorie; Wang, Antonia; Tomazos, Ioannis (Orphanet Journal of Rare Diseases, 2025)