Small molecule treatment alleviates photoreceptor cilia defects in LCA5-deficient human retinal organoids.

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Title: Small molecule treatment alleviates photoreceptor cilia defects in LCA5-deficient human retinal organoids.
Authors: Athanasiou, Dimitra1 (AUTHOR), Afanasyeva, Tess A. V.2 (AUTHOR), Chai, Niuzheng1 (AUTHOR), Ziaka, Kalliopi1 (AUTHOR), Jovanovic, Katarina1 (AUTHOR), Guarascio, Rosellina1 (AUTHOR), Boldt, Karsten3 (AUTHOR), Corral-Serrano, Julio C.1 (AUTHOR), Kanuga, Naheed1 (AUTHOR), Roepman, Ronald2 (AUTHOR), Collin, Rob W. J.2 (AUTHOR), Cheetham, Michael E.1 (AUTHOR) michael.cheetham@ucl.ac.uk
Source: Acta Neuropathologica Communications. 2/11/2025, Vol. 13 Issue 1, p1-16. 16p.
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  Data: Small molecule treatment alleviates photoreceptor cilia defects in LCA5-deficient human retinal organoids.
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  Data: <searchLink fieldCode="JN" term="%22Acta+Neuropathologica+Communications%22">Acta Neuropathologica Communications</searchLink>. 2/11/2025, Vol. 13 Issue 1, p1-16. 16p.
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        Value: 10.1186/s40478-025-01943-y
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      – TitleFull: Small molecule treatment alleviates photoreceptor cilia defects in LCA5-deficient human retinal organoids.
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              Text: 2/11/2025
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