Universal Prime Editing Therapeutic Strategy for RyR1-Related Myopathies: A Protective Mutation Rescues Leaky RyR1 Channel.

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Title: Universal Prime Editing Therapeutic Strategy for RyR1-Related Myopathies: A Protective Mutation Rescues Leaky RyR1 Channel.
Authors: Godbout, Kelly1,2 (AUTHOR) mathieu.dugas@crchudequebec.ulaval.ca, Dugas, Mathieu1,2 (AUTHOR), Reiken, Steven R.3 (AUTHOR), Ramezani, Sina1,2 (AUTHOR), Falle, Alexia1,2 (AUTHOR), Rousseau, Joël2,3 (AUTHOR), Wronska, Anetta E.3 (AUTHOR), Lamothe, Gabriel1,2 (AUTHOR), Canet, Geoffrey1,2 (AUTHOR), Lu, Yaoyao1,2 (AUTHOR), Planel, Emmanuel1,2 (AUTHOR), Marks, Andrew R.3 (AUTHOR), Tremblay, Jacques P.1,2 (AUTHOR) jacques-p.tremblay@crchudequebec.ulaval.ca
Source: International Journal of Molecular Sciences. Apr2025, Vol. 26 Issue 7, p2835. 17p.
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  Data: Universal Prime Editing Therapeutic Strategy for RyR1-Related Myopathies: A Protective Mutation Rescues Leaky RyR1 Channel.
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  Data: <searchLink fieldCode="JN" term="%22International+Journal+of+Molecular+Sciences%22">International Journal of Molecular Sciences</searchLink>. Apr2025, Vol. 26 Issue 7, p2835. 17p.
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