Unlocking the Mysteries of Rare Disease Drug Development: A Beginner's Guide for Clinical Pharmacologists. - Ahmed, Mariam A.; AbuAsal, Bilal; Barrett, Jeffrey S.; Azer, Karim; Hon, Yuen Yi; Albusaysi, Salwa; Shang, Elizabeth; Wang, Meng; Burian, Maria; Rayad, Noha (CTS: Clinical & Translational Science, 2025)