The long-term efficacy of nusinersen on respiratory functions in children with symptomatic spinal muscular atrophy type 1.

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Title: The long-term efficacy of nusinersen on respiratory functions in children with symptomatic spinal muscular atrophy type 1.
Authors: KILIÇ, Mehmet Akif1 mehmetakifkilic1@istanbul.edu.tr, KÜREKÇİ, Fulya1, KİPOĞLU, Osman1, COŞKUN, Orhan1, KARACEBEY, Burçin Nazlı1, KATAR, Selahattin1, AVCI, Rıdvan1, GENÇ, Hülya Maraş1, ÇAKIR, Erkan2, YILDIZ, Edibe Pembegül1
Source: Turkish Journal of Medical Sciences. 2025, Vol. 55 Issue 3, p702-709. 8p.
Database: Academic Search Ultimate
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  Data: The long-term efficacy of nusinersen on respiratory functions in children with symptomatic spinal muscular atrophy type 1.
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  Data: <searchLink fieldCode="JN" term="%22Turkish+Journal+of+Medical+Sciences%22">Turkish Journal of Medical Sciences</searchLink>. 2025, Vol. 55 Issue 3, p702-709. 8p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=186170459
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        Value: 10.55730/1300-0144.6018
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        Text: English
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              Text: 2025
              Type: published
              Y: 2025
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