Tissue distribution of renadirsen sodium, a dystrophin exon-skipping antisense oligonucleotide, in heart and diaphragm after subcutaneous administration to cynomolgus monkeys.

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Title: Tissue distribution of renadirsen sodium, a dystrophin exon-skipping antisense oligonucleotide, in heart and diaphragm after subcutaneous administration to cynomolgus monkeys.
Authors: Yamamura, Naotoshi1 (AUTHOR) yamamura.naotoshib2@daiichisankyo.co.jp, Takakusa, Hideo1 (AUTHOR), Asano, Daigo1 (AUTHOR), Watanabe, Kyoko1 (AUTHOR), Shibaya, Yukari1 (AUTHOR), Yamanaka, Ryo2 (AUTHOR), Fusegawa, Keiichi2 (AUTHOR), Kanda, Akira3 (AUTHOR), Nagase, Hiroyuki3 (AUTHOR), Takaishi, Kiyosumi3 (AUTHOR), Koizumi, Makoto4 (AUTHOR), Takeshima, Yasuhiro5 (AUTHOR), Matsuo, Masafumi6 (AUTHOR)
Source: Nucleosides, Nucleotides & Nucleic Acids. 2025, Vol. 44 Issue 8, p626-642. 17p.
Database: Academic Search Ultimate
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ISSN:15257770
DOI:10.1080/15257770.2024.2389545