In vivo applications and toxicities of AAV-based gene therapies in rare diseases.

Saved in:
Bibliographic Details
Title: In vivo applications and toxicities of AAV-based gene therapies in rare diseases.
Authors: Zhao, Qian1 (AUTHOR), Peng, Huifang1 (AUTHOR), Ma, Yujin1 (AUTHOR), Yuan, Huijun2 (AUTHOR) yuanhj301@wchscu.cn, Jiang, Hongwei1 (AUTHOR) jianghw@haust.edu.cn
Source: Orphanet Journal of Rare Diseases. 7/17/2025, Vol. 20 Issue 1, p1-14. 14p.
Database: Academic Search Ultimate
Full text is not displayed to guests.
FullText Links:
  – Type: pdflink
Text:
  Availability: 1
Header DbId: asn
DbLabel: Academic Search Ultimate
An: 186711649
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: In vivo applications and toxicities of AAV-based gene therapies in rare diseases.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AR" term="%22Zhao%2C+Qian%22">Zhao, Qian</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Peng%2C+Huifang%22">Peng, Huifang</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Ma%2C+Yujin%22">Ma, Yujin</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Yuan%2C+Huijun%22">Yuan, Huijun</searchLink><relatesTo>2</relatesTo> (AUTHOR)<i> yuanhj301@wchscu.cn</i><br /><searchLink fieldCode="AR" term="%22Jiang%2C+Hongwei%22">Jiang, Hongwei</searchLink><relatesTo>1</relatesTo> (AUTHOR)<i> jianghw@haust.edu.cn</i>
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 7/17/2025, Vol. 20 Issue 1, p1-14. 14p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=186711649
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1186/s13023-025-03893-z
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        PageCount: 14
        StartPage: 1
    Titles:
      – TitleFull: In vivo applications and toxicities of AAV-based gene therapies in rare diseases.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Zhao, Qian
      – PersonEntity:
          Name:
            NameFull: Peng, Huifang
      – PersonEntity:
          Name:
            NameFull: Ma, Yujin
      – PersonEntity:
          Name:
            NameFull: Yuan, Huijun
      – PersonEntity:
          Name:
            NameFull: Jiang, Hongwei
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 17
              M: 07
              Text: 7/17/2025
              Type: published
              Y: 2025
          Identifiers:
            – Type: issn-print
              Value: 17501172
          Numbering:
            – Type: volume
              Value: 20
            – Type: issue
              Value: 1
          Titles:
            – TitleFull: Orphanet Journal of Rare Diseases
              Type: main
ResultId 1