CRISPR/Cas-Based Ex Vivo Gene Therapy and Lysosomal Storage Disorders: A Perspective Beyond Cas9.

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Bibliographic Details
Title: CRISPR/Cas-Based Ex Vivo Gene Therapy and Lysosomal Storage Disorders: A Perspective Beyond Cas9.
Authors: Leal, Andrés Felipe1,2,3 (AUTHOR) luis.prieto.va@fvl.org.co, Prieto, Luis Eduardo2 (AUTHOR), Pachajoa, Harry1,2,3,4 (AUTHOR) hmpachajoa@icesi.edu.co
Source: Cells (2073-4409). Aug2025, Vol. 14 Issue 15, p1147. 20p.
Database: Academic Search Ultimate
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ISSN:20734409
DOI:10.3390/cells14151147