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Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data.

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Title: Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data.
Authors: Toro, Walter1 (AUTHOR) walter.toro_jimenez@novartis.com, Reyna, Sandra P.1 (AUTHOR), Ritter, Shannon1 (AUTHOR), Patel, Anish1 (AUTHOR), Mumneh, Nayla1 (AUTHOR), Dabbous, Omar1 (AUTHOR)
Source: Neurology & Therapy. Oct2025, Vol. 14 Issue 5, p1903-1918. 16p.
Database: Academic Search Ultimate
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  Data: Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data.
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  Data: <searchLink fieldCode="JN" term="%22Neurology+%26+Therapy%22">Neurology & Therapy</searchLink>. Oct2025, Vol. 14 Issue 5, p1903-1918. 16p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=188124840
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        Value: 10.1007/s40120-025-00791-1
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        Text: English
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        StartPage: 1903
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      – TitleFull: Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data.
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            – D: 01
              M: 10
              Text: Oct2025
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              Y: 2025
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