Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data. - Toro, Walter; Reyna, Sandra P.; Ritter, Shannon; Patel, Anish; Mumneh, Nayla; Dabbous, Omar (Neurology & Therapy, 2025)