Adenine base editing rescues disrupted BCKDH function and reduces BCAAs toxic accumulation in maple syrup urine disease patient iPSC-hepatic organoids. - Zhang, Haiyan; Wan, Zirui; Li, Xiaomei; Wang, Bin; Guan, Jingyun; Li, Yue; Jin, Xiaohua; Ma, Xu; Liu, Guohua (Stem Cell Research & Therapy, 2025)