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Safety and efficacy of laronidase in Chinese patients with mucopolysaccharidosis type I: a phase IV, single-arm, open-label, multicenter study.

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Title: Safety and efficacy of laronidase in Chinese patients with mucopolysaccharidosis type I: a phase IV, single-arm, open-label, multicenter study.
Authors: Liang, Yan1,2 (AUTHOR), Yang, Yan-Ling3 (AUTHOR), Zou, Chao-Chun4 (AUTHOR), Liu, Li5 (AUTHOR), Jiao, Ying6 (AUTHOR), Wang, Yu7,8 (AUTHOR), Liu, Xin7 (AUTHOR), Luo, Xiao-Ping1,2 (AUTHOR) xpluo@tjh.tjmu.edu.cn
Source: Orphanet Journal of Rare Diseases. 10/29/2025, Vol. 20 Issue 1, p1-10. 10p.
Database: Academic Search Ultimate
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An: 188948627
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PubType: Academic Journal
PubTypeId: academicJournal
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  Data: Safety and efficacy of laronidase in Chinese patients with mucopolysaccharidosis type I: a phase IV, single-arm, open-label, multicenter study.
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  Data: <searchLink fieldCode="AR" term="%22Liang%2C+Yan%22">Liang, Yan</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Yang%2C+Yan-Ling%22">Yang, Yan-Ling</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Zou%2C+Chao-Chun%22">Zou, Chao-Chun</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Liu%2C+Li%22">Liu, Li</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Jiao%2C+Ying%22">Jiao, Ying</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Wang%2C+Yu%22">Wang, Yu</searchLink><relatesTo>7,8</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Liu%2C+Xin%22">Liu, Xin</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Luo%2C+Xiao-Ping%22">Luo, Xiao-Ping</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<i> xpluo@tjh.tjmu.edu.cn</i>
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 10/29/2025, Vol. 20 Issue 1, p1-10. 10p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=188948627
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        Value: 10.1186/s13023-025-04056-w
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        Text: English
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      – TitleFull: Safety and efficacy of laronidase in Chinese patients with mucopolysaccharidosis type I: a phase IV, single-arm, open-label, multicenter study.
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            NameFull: Liang, Yan
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            NameFull: Yang, Yan-Ling
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              Text: 10/29/2025
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              Y: 2025
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            – TitleFull: Orphanet Journal of Rare Diseases
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