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Long-term outcomes of elosulfase alfa enzyme replacement therapy in adults with MPS IVA: a sub-analysis of the Morquio A Registry Study (MARS).

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Title: Long-term outcomes of elosulfase alfa enzyme replacement therapy in adults with MPS IVA: a sub-analysis of the Morquio A Registry Study (MARS).
Authors: Stepien, Karolina M.1 (AUTHOR) karolina.stepien@nca.nhs.uk, Burton, Barbara K.2 (AUTHOR), Bober, Michael B.3 (AUTHOR), Campeau, Philippe M.4 (AUTHOR), Ellaway, Carolyn5 (AUTHOR), Bhattacharya, Kaustuv5 (AUTHOR), Guffon, Nathalie6 (AUTHOR), Hinds, David7 (AUTHOR), Hunt, Abigail7 (AUTHOR), Lail, Alice7 (AUTHOR), Lin, Shuan-Pei8 (AUTHOR), Magner, Martin9 (AUTHOR), Murphy, Elaine10 (AUTHOR), Reisewitz, Pascal7 (AUTHOR), Mitchell, John J.11 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 10/30/2025, Vol. 20 Issue 1, p1-10. 10p.
Database: Academic Search Ultimate
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An: 189004365
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  Data: Long-term outcomes of elosulfase alfa enzyme replacement therapy in adults with MPS IVA: a sub-analysis of the Morquio A Registry Study (MARS).
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 10/30/2025, Vol. 20 Issue 1, p1-10. 10p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=189004365
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        Value: 10.1186/s13023-025-04064-w
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        Text: English
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              Text: 10/30/2025
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