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Medical expenses and care pathways of patients with Pompe receiving myozyme: an observational study based on the French national healthcare database.

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Title: Medical expenses and care pathways of patients with Pompe receiving myozyme: an observational study based on the French national healthcare database.
Authors: Le Bras, Alicia1 (AUTHOR) alicia.le-bras@aphp.fr, De Lonlay, Pascale2 (AUTHOR), Attarian, Shahram3 (AUTHOR), Brassier, Anaïs4 (AUTHOR), Durand-Zaleski, Isabelle1,5,6 (AUTHOR), Laforêt, Pascal7 (AUTHOR), Arrassi, Azzeddine (AUTHOR), Bedat-Millet, Anne-Laure (AUTHOR), Béhin, Anthony (AUTHOR), Beltran, Stéphane (AUTHOR), Bouibede, Françoise Bouhour Fatima (AUTHOR), Caillaud, Catherine (AUTHOR), Chabrol, Brigitte (AUTHOR), Champeaux, Murielle (AUTHOR), Cintas, Pascal (AUTHOR), Davion, Jean-Baptiste (AUTHOR), Diab, Eva (AUTHOR), Deibener-Kaminsky, Joelle (AUTHOR), Demurger, Florence (AUTHOR), Espil, Caroline (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 10/31/2025, Vol. 20 Issue 1, p1-9. 9p.
Database: Academic Search Ultimate
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  Data: Medical expenses and care pathways of patients with Pompe receiving myozyme: an observational study based on the French national healthcare database.
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 10/31/2025, Vol. 20 Issue 1, p1-9. 9p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=189054306
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              Text: 10/31/2025
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