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Mitigating the impact of study-start delays in clinical trials for rare disorders: insights and lessons from a PKAN trial.

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Title: Mitigating the impact of study-start delays in clinical trials for rare disorders: insights and lessons from a PKAN trial.
Authors: Bracke, Marleen M. G.1,2 (AUTHOR) m.m.g.bracke@umcg.nl, Polet, Sjoukje S.1 (AUTHOR) s.s.polet@umcg.nl, Plantinga, Mirjam3 (AUTHOR) m.plantinga@umcg.nl, de Koning, Tom J.1,3,4 (AUTHOR) tom.j_de_koning@med.lu.se
Source: Orphanet Journal of Rare Diseases. 11/11/2025, Vol. 20 Issue 1, p1-13. 13p.
Database: Academic Search Ultimate
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  Data: Mitigating the impact of study-start delays in clinical trials for rare disorders: insights and lessons from a PKAN trial.
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 11/11/2025, Vol. 20 Issue 1, p1-13. 13p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=189234857
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        Value: 10.1186/s13023-025-04035-1
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      – Code: eng
        Text: English
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      – TitleFull: Mitigating the impact of study-start delays in clinical trials for rare disorders: insights and lessons from a PKAN trial.
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            NameFull: Polet, Sjoukje S.
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              Text: 11/11/2025
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              Y: 2025
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