A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies.

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Title: A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies.
Authors: Wilk, Jordan1,2 (AUTHOR), Aggarwal, Varun3 (AUTHOR), Pauley, Mike3 (AUTHOR), Corey, Diane3 (AUTHOR), Conrado, Daniela J.4 (AUTHOR), Lingineni, Karthik5 (AUTHOR), Morales, Juan Francisco1,3 (AUTHOR), Yoon, Deok Yong1 (AUTHOR), Zhang, Yi3 (AUTHOR), Cui, Zihan3 (AUTHOR), Burton, Jackson6 (AUTHOR), Larkindale, Jane3 (AUTHOR), Ma, Shu Chin3 (AUTHOR), Hovinga, Collin3 (AUTHOR), Martinez, Terina3 (AUTHOR), Romero, Klaus3 (AUTHOR), Belfiore‐Oshan, Ramona3 (AUTHOR), Kim, Sarah1 (AUTHOR) sarahkim@cop.ufl.edu
Source: CPT: Pharmacometrics & Systems Pharmacology. Nov2025, Vol. 14 Issue 11, p1787-1796. 10p.
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PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=189393127
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              Text: Nov2025
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