Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients.

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Title: Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients.
Authors: Sips, Fianne1 (AUTHOR), Virgolin, Marco1 (AUTHOR), Pasculli, Giuseppe2 (AUTHOR), Reali, Federico3 (AUTHOR), Paris, Alessio3 (AUTHOR), Janus, Annette4 (AUTHOR), Godfrin, Yann4 (AUTHOR), Röshammar, Daniel2 (AUTHOR), Marchetti, Luca3,5 (AUTHOR), Knöchel, Jane2 (AUTHOR) jane.knochel@insilicotrials.com
Source: CPT: Pharmacometrics & Systems Pharmacology. Nov2025, Vol. 14 Issue 11, p1739-1742. 4p.
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  Data: Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients.
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  Data: <searchLink fieldCode="AR" term="%22Sips%2C+Fianne%22">Sips, Fianne</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Virgolin%2C+Marco%22">Virgolin, Marco</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Pasculli%2C+Giuseppe%22">Pasculli, Giuseppe</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Reali%2C+Federico%22">Reali, Federico</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Paris%2C+Alessio%22">Paris, Alessio</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Janus%2C+Annette%22">Janus, Annette</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Godfrin%2C+Yann%22">Godfrin, Yann</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Röshammar%2C+Daniel%22">Röshammar, Daniel</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Marchetti%2C+Luca%22">Marchetti, Luca</searchLink><relatesTo>3,5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Knöchel%2C+Jane%22">Knöchel, Jane</searchLink><relatesTo>2</relatesTo> (AUTHOR)<i> jane.knochel@insilicotrials.com</i>
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  Data: <searchLink fieldCode="JN" term="%22CPT%3A+Pharmacometrics+%26+Systems+Pharmacology%22">CPT: Pharmacometrics & Systems Pharmacology</searchLink>. Nov2025, Vol. 14 Issue 11, p1739-1742. 4p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=189393136
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              Text: Nov2025
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