Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients.
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| Title: | Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients. |
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| Authors: | Sips, Fianne1 (AUTHOR), Virgolin, Marco1 (AUTHOR), Pasculli, Giuseppe2 (AUTHOR), Reali, Federico3 (AUTHOR), Paris, Alessio3 (AUTHOR), Janus, Annette4 (AUTHOR), Godfrin, Yann4 (AUTHOR), Röshammar, Daniel2 (AUTHOR), Marchetti, Luca3,5 (AUTHOR), Knöchel, Jane2 (AUTHOR) jane.knochel@insilicotrials.com |
| Source: | CPT: Pharmacometrics & Systems Pharmacology. Nov2025, Vol. 14 Issue 11, p1739-1742. 4p. |
| Database: | Academic Search Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 189393136 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Sips%2C+Fianne%22">Sips, Fianne</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Virgolin%2C+Marco%22">Virgolin, Marco</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Pasculli%2C+Giuseppe%22">Pasculli, Giuseppe</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Reali%2C+Federico%22">Reali, Federico</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Paris%2C+Alessio%22">Paris, Alessio</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Janus%2C+Annette%22">Janus, Annette</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Godfrin%2C+Yann%22">Godfrin, Yann</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Röshammar%2C+Daniel%22">Röshammar, Daniel</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Marchetti%2C+Luca%22">Marchetti, Luca</searchLink><relatesTo>3,5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Knöchel%2C+Jane%22">Knöchel, Jane</searchLink><relatesTo>2</relatesTo> (AUTHOR)<i> jane.knochel@insilicotrials.com</i> – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22CPT%3A+Pharmacometrics+%26+Systems+Pharmacology%22">CPT: Pharmacometrics & Systems Pharmacology</searchLink>. Nov2025, Vol. 14 Issue 11, p1739-1742. 4p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=189393136 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1002/psp4.70096 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 4 StartPage: 1739 Titles: – TitleFull: Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Sips, Fianne – PersonEntity: Name: NameFull: Virgolin, Marco – PersonEntity: Name: NameFull: Pasculli, Giuseppe – PersonEntity: Name: NameFull: Reali, Federico – PersonEntity: Name: NameFull: Paris, Alessio – PersonEntity: Name: NameFull: Janus, Annette – PersonEntity: Name: NameFull: Godfrin, Yann – PersonEntity: Name: NameFull: Röshammar, Daniel – PersonEntity: Name: NameFull: Marchetti, Luca – PersonEntity: Name: NameFull: Knöchel, Jane IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 11 Text: Nov2025 Type: published Y: 2025 Identifiers: – Type: issn-print Value: 21638306 Numbering: – Type: volume Value: 14 – Type: issue Value: 11 Titles: – TitleFull: CPT: Pharmacometrics & Systems Pharmacology Type: main |
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